Severe Lipodystrophy Following Prolonged Subcutaneous Administration of Antisense Oligonucleotides

Severe Lipodystrophy Following Prolonged Subcutaneous Administration of Antisense Oligonucleotides

This case report describes a severe adverse event following antisense oligonucleotide treatment for muscular dystrophy that occurred in 6 pediatric patients.

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Bibliographische Detailangaben
Veröffentlicht in:Archives of dermatology (1960) 2019-09, Vol.155 (9), p.1084-1086
Hauptverfasser: Nguyen, Anh Ly, Morren, Marie-Anne, van Doorn, Remco
Format: Artikel
Sprache:eng
Schlagworte:
Medical treatment
Muscular dystrophy
Neuromuscular diseases
Pediatrics
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Beschreibung
Zusammenfassung:This case report describes a severe adverse event following antisense oligonucleotide treatment for muscular dystrophy that occurred in 6 pediatric patients.
ISSN:2168-6068
2168-6084
DOI:10.1001/jamadermatol.2019.1404