IDURONIDASE STABILIZERS AND USES THEREOF

Disclosed herein are compounds that stabilize recombinant human α-iduronidase (rh-α-IDUA) activity, and their uses in the treatment and/or prophylaxis of lysosomal storage diseases (LSDs), such as mucopolysaccharidosis type I (MPS1). The compound disclosed herein has the structure of formula (I), wh...

Ausführliche Beschreibung

Bibliographische Detailangaben

Hauptverfasser:	TENG, Hsuan-Hsuan, LIN, Hung-Yi, CHANG, Shih-Ying, WU, Hsi-Ju, CHENG, Wei-Chieh
Format:	Patent
Sprache:	eng ; fre
Schlagworte:	HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
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