IN VIVO LENTIVIRAL GENE THERAPY FOR THE TREATMENT OF PRIMARY HYPEROXALURIA TYPE 1

The present invention relates to a lentivirus vector (LV) comprising a nucleic acid, wherein the nucleic acid comprises a transcriptional unit which comprises, from 5' to 3', an hepatocyte-specific promoter, preferably a ET promoter, a nucleotide sequence encoding the optimized Alanine-Gly...

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Bibliographische Detailangaben
Hauptverfasser:	GARCÍA TORRALBA, Aida, GARCÍA BRAVO, María, MOLINOS VICENTE, Andrea, SEGOVIA SANZ, José Carlos, NIETO ROMERO, Virginia
Format:	Patent
Sprache:	eng ; fre
Schlagworte:	BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS SPIRITS VINEGAR WINE
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