NOVEL COMPOUNDS FOR TREATMENT OF DISEASES RELATED TO DUX4 EXPRESSION

The present invention relates to compounds that act as DUX4 repressors, suitable for the treatment of diseases related to DUX4 expression, such as muscular dystrophies. It also relates to use of such compounds, or to methods of use of such compounds. La présente invention concerne des composés agiss...

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Bibliographische Detailangaben
Hauptverfasser:	ANIGHORO, Andrew, PACE, Robert David Matthew, FOULKES, Gregory, RICHARDS, Jonathan Philip, LOKE, Pui Leng, DE MAEYER, Joris Herman, DAVENPORT, Adam James, DICKIE, Anthony Paul, RUEDA-ZUBIAURRE, Ainoa, ELLWOOD, Simon Fletcher, SCHNORRENBERG, Gerd, LECCI, Cristina
Format:	Patent
Sprache:	eng ; fre
Schlagworte:	CHEMISTRY HETEROCYCLIC COMPOUNDS HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE METALLURGY ORGANIC CHEMISTRY PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
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Beschreibung
Zusammenfassung:	The present invention relates to compounds that act as DUX4 repressors, suitable for the treatment of diseases related to DUX4 expression, such as muscular dystrophies. It also relates to use of such compounds, or to methods of use of such compounds. La présente invention concerne des composés agissant comme des répresseurs de DUX4 adaptés au traitement des maladies liées à l'expression de DUX4, telles que les dystrophies musculaires. La présente invention concerne également l'utilisation de tels composés, ou des procédés d'utilisation de tels composés.