ANTISENSE OLIGONUCLEOTIDES RESCUE ABERRANT SPLICING OF ABCA4

The present invention relates to the field of medicine. In particular, it relates to novel antisense oligonucleotides that may be used in the treatment, prevention and/or delay of Stargardt disease. La présente invention concerne le domaine de la médecine. En particulier, l'invention concerne d...

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Hauptverfasser:	COLLIN, Robert Wilhelmus Johanna, GARANTO IGLESIAS, Alejandro, CREMERS, Franciscus Peter Maria
Format:	Patent
Sprache:	eng ; fre
Schlagworte:	BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPIRITS VINEGAR WINE
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Beschreibung
Zusammenfassung:	The present invention relates to the field of medicine. In particular, it relates to novel antisense oligonucleotides that may be used in the treatment, prevention and/or delay of Stargardt disease. La présente invention concerne le domaine de la médecine. En particulier, l'invention concerne de nouveaux oligonucléotides antisens qui peuvent être utilisés dans le traitement, la prévention et/ou le retardement de la maladie de Stargardt.