METHODS AND COMPOSITIONS FOR EXPRESSING PHENYLALANINE HYDROXYLASE
The present disclosure provides expression constructs comprising a phenylalanine hydroxylase (PAH) transgene and methods of using the constructs for treating phenylketonuria (PKU).
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Format: | Patent |
Sprache: | eng |
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Zusammenfassung: | The present disclosure provides expression constructs comprising a phenylalanine hydroxylase (PAH) transgene and methods of using the constructs for treating phenylketonuria (PKU). |
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