COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE

The present disclosure relates to pharmaceutical compositions of adeno-associated viral (AAV) particles encoding siRNA molecules and methods for treating Huntington's Disease (HD).

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Bibliographische Detailangaben
Hauptverfasser: Sah, Dinah Wen-Yee, Carter, Todd, Hersch, Steven M, Karpes, Lori B, Thompson, Jeffrey S, Carroll Soper, Jenna, Liu, Bin, Cardinal, Jacob J, Zhou, Pengcheng, Gamba-Vitalo, Christina
Format: Patent
Sprache:eng
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Zusammenfassung:The present disclosure relates to pharmaceutical compositions of adeno-associated viral (AAV) particles encoding siRNA molecules and methods for treating Huntington's Disease (HD).