COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES

The present invention is directed to genome editing systems, reagents and methods for the treatment of hemoglobinopathies.

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Bibliographische Detailangaben
Hauptverfasser: SNEAD, Jennifer, Stevenson, Susan, YANG, Yi, SCHMEDT, Christian, MICKANIN, Craig Stephen
Format: Patent
Sprache:eng
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Beschreibung
Zusammenfassung:The present invention is directed to genome editing systems, reagents and methods for the treatment of hemoglobinopathies.