NOVEL COMPOUNDS FOR TREATMENT OF CYSTIC FIBROSIS

A corrector agent capable of stabilizing a newly synthesized cystic fibrosis transmembrane conductance regulator (CFTR) protein, useful in the treatment of cystic fibrosis. Un agente corrector capaz de estabilizar una proteína reguladora de la conductancia transmembrana en la fibrosis quística (CFTR...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Hauptverfasser: Brian S. BROWN, Nicolas DESROY, Sachin V. PATEL, Douglas CYR, Xueqing WANG, Koen Karel JANSEN, Jianguo JI, Adeline Marie Elise PALISSE, Jean-michel LEFRANCOIS, Gert Jules Hector DE WILDE, Mathieu Rafaël PIZZONERO, Rhalid AKKARI, Steven Emiel VAN DER PLAS, Philip R. KYM, Luke Jonathan ALVEY, Chris TSE, Pieter Isabelle Roger CLAES, Anurupa SHRESTHA, Elsa DE LEMOS, Gregory A. GFESSER, Romain Luc Marie GOSMINI, Xavier Marie BOCK, Katja E. CONRATH, Christel Jeanne Marie MENET, Oscar MAMMOLITI, Marlon D. COWART, Nuria Merayo MERAYO, Christopher Gaëtan HOUSSEMAN, Elizabeth C. SWIFT, Gregory John Robert NEWSOME, Béranger DUTHION
Format: Patent
Sprache:eng ; spa
Schlagworte:
Online-Zugang:Volltext bestellen
Tags: Tag hinzufügen
Keine Tags, Fügen Sie den ersten Tag hinzu!
Beschreibung
Zusammenfassung:A corrector agent capable of stabilizing a newly synthesized cystic fibrosis transmembrane conductance regulator (CFTR) protein, useful in the treatment of cystic fibrosis. Un agente corrector capaz de estabilizar una proteína reguladora de la conductancia transmembrana en la fibrosis quística (CFTR) recién sintetizada, útil en el tratamiento de la fibrosis quística.