COMPOUNDS FOR USE IN THE TREATMENT OF DISEASES BASED ON THE EXPRESSION OF TOXIC TRANSCRIPTS
Compounds to be used in the treatment of diseases based on the expression of toxic transcripts. The present invention relates to peptide molecules, specifically hexapeptides, designed for the prevention and/or treatment of diseases the etiology whereof is based on the presence of toxic transcripts t...
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Zusammenfassung: | Compounds to be used in the treatment of diseases based on the expression of toxic transcripts. The present invention relates to peptide molecules, specifically hexapeptides, designed for the prevention and/or treatment of diseases the etiology whereof is based on the presence of toxic transcripts that comprise CUG, CCUG, CGG, CAG and AAG repeats, preferably: DM1 SCA8, DM2, FXTAS, HD and FA.
Compuestos para ser usados en el tratamiento de enfermedades basadas en la expresión de transcritos tóxicos con repeticiones CUG o CCUG. La presente invención hace referencia a moléculas peptídicas, concretamente hexapéptidos, para la prevención y/o tratamiento de enfermedades cuya etiología se basa en la presencia de transcritos tóxicos que comprenden repeticiones CUG o CCUG, preferentemente: DM1, DM2 y SCA8. |
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