LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY

Disclosed herein are compositions and methods for modulating the production of a protein in a target cell. The compositions and methods disclosed herein are capable of ameliorating diseases associated with protein or enzyme deficiencies.

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Bibliographische Detailangaben
Hauptverfasser: DEROSA, Frank, GUILD, Braydon Charles, HEARTLEIN, Michael
Format: Patent
Sprache:eng ; fre ; ger
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Beschreibung
Zusammenfassung:Disclosed herein are compositions and methods for modulating the production of a protein in a target cell. The compositions and methods disclosed herein are capable of ameliorating diseases associated with protein or enzyme deficiencies.