PAH-MODULATING COMPOSITIONS AND METHODS

The disclosure provides, e.g., compositions, systems, and methods for targeting, editing, modifying, or manipulating a host cell's genome at one or more locations in a DNA sequence in a cell, tissue, or subject. Gene modifying systems for treating phenylketonuria (PKU) are described.

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Bibliographische Detailangaben
Hauptverfasser:	ALTSHULER, Robert Charles, STEINBERG, Barrett Ethan, QUERBES, William, COTTA-RAMUSINO, Cecilia Giovanna Silvia, ROQUET, Nathaniel, SALOMON, William Edward, CITORIK, Robert James, KOTLAR, Randi Michelle, WANG, Zhan, RAY, Ananya, SANCHEZ, Carlos, KIM, Kyusik, CHEE, Daniel Raymond, APPONI, Luciano Henrique, BOTHMER, Anne Helen, MCALLISTER, Gregory David
Format:	Patent
Sprache:	eng ; fre ; ger
Schlagworte:	BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPIRITS VINEGAR WINE
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Beschreibung
Zusammenfassung:	The disclosure provides, e.g., compositions, systems, and methods for targeting, editing, modifying, or manipulating a host cell's genome at one or more locations in a DNA sequence in a cell, tissue, or subject. Gene modifying systems for treating phenylketonuria (PKU) are described.