ANTISENSE OLIGONUCLEOTIDES TARGETING THE EXON 51 OF DYSTROPHIN GENE

Provided are splice-switching hydroxyalkoxylated antisense oligonucleotides for preventing, treating, and/or delaying neuromuscular disorders, more specifically Duchenne Muscular Dystrophy.

Gespeichert in:

Bibliographische Detailangaben
Hauptverfasser:	VAN DEUTEKOM, Judith Christina Theodora, DE VISSER, Peter Christian
Format:	Patent
Sprache:	eng ; fre ; ger
Schlagworte:	BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPIRITS VINEGAR WINE
Online-Zugang:	Volltext bestellen
Tags:	Tag hinzufügen Keine Tags, Fügen Sie den ersten Tag hinzu!

Beschreibung
Zusammenfassung:	Provided are splice-switching hydroxyalkoxylated antisense oligonucleotides for preventing, treating, and/or delaying neuromuscular disorders, more specifically Duchenne Muscular Dystrophy.