MEANS AND METHODS FOR COUNTERACTING MUSCLE DISORDERS

The invention relates a method wherein a molecule is used for inducing and/or promoting skipping of at least one of exon 43, exon 46, exons 50-53 of the DMD premRNA in a patient, preferably in an isolated cell of a patient, the method comprising providing said cell and/or said patient with a molecul...

Ausführliche Beschreibung

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Bibliographische Detailangaben
Hauptverfasser:	Platenburg, Gerardus Johannes, van Deutekom, Judith Christina Theodora, van Ommen, Garrit-Jan Boudewijn, de Kimpe, Josephus Johannes, Aartsma-Rus, Annemieke
Format:	Patent
Sprache:	eng ; fre ; ger
Schlagworte:	HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
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Beschreibung
Zusammenfassung:	The invention relates a method wherein a molecule is used for inducing and/or promoting skipping of at least one of exon 43, exon 46, exons 50-53 of the DMD premRNA in a patient, preferably in an isolated cell of a patient, the method comprising providing said cell and/or said patient with a molecule. The invention also relates to said molecule as such.