ADENOASSOCIATED VIRUS VECTORS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS

The present invention provides new adenoassociated virus vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIIB. La présente invention concerne de nouveaux vecteurs dérivés de vi...

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Bibliographische Detailangaben
Hauptverfasser:	RIBERA SANCHEZ, ALBERT, BOSCH TUBERT, M FATIMA, HAURIGOT MENDOCA, M VIRGINIA
Format:	Patent
Sprache:	eng ; fre
Schlagworte:	BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS SPIRITS VINEGAR WINE
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Beschreibung
Zusammenfassung:	The present invention provides new adenoassociated virus vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type IIIB. La présente invention concerne de nouveaux vecteurs dérivés de virus adéno-associés et des compositions pharmaceutiques les contenant, destinées au traitement de troubles du stockage lysosomal, et en particulier, au traitement de la mucopolysaccharidose de type IIIB.