RECOMBINANT HUMAN ACID ALPHA-GLUCOSIDASE AND USES THEREOF

Provided herein are methods of treating Pompe disease comprising administering a population of recombinant human acid a-glucosidase molecules or a pharmaceutical composition or formulation thereof, and a pharmacological chaperone.

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Bibliographische Detailangaben
Hauptverfasser: DO, Hung, BARTH, Jay, GOTSCHALL, Russell, CHAR, Hing
Format: Patent
Sprache:eng
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Beschreibung
Zusammenfassung:Provided herein are methods of treating Pompe disease comprising administering a population of recombinant human acid a-glucosidase molecules or a pharmaceutical composition or formulation thereof, and a pharmacological chaperone.