Outcome following Gene Therapy in Patients with Severe Wiskott-Aldrich Syndrome
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| Veröffentlicht in: | JAMA : the journal of the American Medical Association 2015-04, Vol.313 (15), p.1550-1563 |
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| container_end_page | 1563 |
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| container_issue | 15 |
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| container_title | JAMA : the journal of the American Medical Association |
| container_volume | 313 |
| creator | Abina, Salima Hacein-Bey Gaspar, H. Bobby Blondeau, Johanna Caccavelli, Laure Charrier, Sabine Buckland, Karen Picard, Capucine Six, Emmanuelle Himoudi, Nourredine Gilmour, Kimberly McNicol, Anne-Marie Hara, Havinder Xu-Bayford, Jinhua Rivat, Christine Touzot, Fabien Mavilio, Fulvio Lim, Annick Treluyer, Jean-Marc Héritier, Sébastien Lefrere, Francois Magalon, Jeremy Pengue-Koyi, Isabelle Honnet, Géraldine Blanche, Stéphane Sherman, Eric A. Male, Frances Berry, Charles Malani, Nirav Bushman, Frederic D. Fischer, Alain Thrasher, Adrian J. Galy, Anne Cavazzana, Marina |
| description | |
| doi_str_mv | 10.1001/jama.2015.3253 |
| format | Article |
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| ispartof | JAMA : the journal of the American Medical Association, 2015-04, Vol.313 (15), p.1550-1563 |
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| language | eng |
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| source | American Medical Association Journals |
| title | Outcome following Gene Therapy in Patients with Severe Wiskott-Aldrich Syndrome |
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