Novel outcome measures for clinical trials in cystic fibrosis

Summary Cystic fibrosis (CF) is a common inherited condition caused by mutations in the gene encoding the CF transmembrane regulator protein. With increased understanding of the molecular mechanisms underlying CF and the development of new therapies there comes the need to develop new outcome measur...

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Veröffentlicht in:	Pediatric pulmonology 2015-03, Vol.50 (3), p.302-315
Hauptverfasser:	Tiddens, Harm A.W.M., Puderbach, Michael, Venegas, Jose G., Ratjen, Felix, Donaldson, Scott H., Davis, Stephanie D., Rowe, Steven M., Sagel, Scott D., Higgins, Mark, Waltz, David A.
Format:	Artikel
Sprache:	eng
Schlagworte:	CFTR activity cystic fibrosis endpoints imaging outcome measures Reviews sputum biomarkers
Online-Zugang:	Volltext
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