A phase I/II study of tgAAV-CF for the treatment of chronic sinusitis in patients with cystic fibrosis

Cystic fibrosis (CF) is the most common serious autosomal recessive disease, affecting between 1 and 2,000 and 1 in 4,500 children of Caucasian origin. The main characteristics of CF are malabsorption due to exocrine pancreatic insufficiency, recurrent bacterial infections of the lower exocrine panc...

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