Plasma miRNAs Correlate with Structural Brain and Cardiac Damage in Friedreich’s Ataxia

Friedreich’s Ataxia (FRDA) is the most common autosomal recessive ataxia worldwide and is caused by biallelic unstable intronic GAA expansions at FXN . With its limited therapy and the recent approval of the first disease-modifying agent for FRDA, the search for biological markers is urgently needed...

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