Spinal presentations in children with spinal muscular atrophy type 1 following gene therapy treatment with onasemnogene abeparvovec – The SMA REACH UK network experience

•Spinal asymmetry and kyphosis are common in gene therapy treated SMA 1 patients.•It is important to develop spinal monitoring pathways for this cohort of patients.•Preventative TLSO use significantly reduces incidence of spinal asymmetry.•Spinal surgery may be required in a substantial proportion o...

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