A call to arms against ultra-rare diseases
The not-for profit foundation n-Lorem seeks to provide experimental antisense oligonucleotide treatments to patients with ultra-rare disease free for their entire lifetime.
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| Veröffentlicht in: | Nature biotechnology 2021-06, Vol.39 (6), p.671-677 |
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| container_end_page | 677 |
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| container_issue | 6 |
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| container_title | Nature biotechnology |
| container_volume | 39 |
| creator | Crooke, Stanley T. |
| description | The not-for profit foundation n-Lorem seeks to provide experimental antisense oligonucleotide treatments to patients with ultra-rare disease free for their entire lifetime. |
| doi_str_mv | 10.1038/s41587-021-00945-0 |
| format | Article |
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| identifier | ISSN: 1087-0156 |
| ispartof | Nature biotechnology, 2021-06, Vol.39 (6), p.671-677 |
| issn | 1087-0156 1546-1696 |
| language | eng |
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| source | Nature Journals Online; SpringerLink Journals - AutoHoldings |
| subjects | 692/699 706/648 Agriculture Aims and objectives Antisense oligonucleotides Bioinformatics Biomedical and Life Sciences Biomedical Engineering/Biotechnology Biomedicine Biotechnology Comment Disease Finance Foundations (Endowments) Good Manufacturing Practice Life Sciences Medical research Medicine, Experimental Mutation Patients Rare diseases |
| title | A call to arms against ultra-rare diseases |
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