Adeno-Associated Virus Vector for Central Nervous System Gene Therapy

The past several years have witnessed significant advances in the development of therapeutic gene delivery for neurological disorders of the central nervous system (CNS). In particular, genome-wide sequencing analysis has deepened our understanding of mutations that underlie many monogenic disorders...

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Veröffentlicht in:	Trends in molecular medicine 2021-06, Vol.27 (6), p.524-537
Hauptverfasser:	Zhu, Danqing, Schieferecke, Adam J., Lopez, Paola A., Schaffer, David V.
Format:	Artikel
Sprache:	eng
Schlagworte:	AAV Animals Central Nervous System Diseases - genetics Central Nervous System Diseases - therapy CNS Dependovirus - genetics gene therapy Genetic Therapy - methods Genetic Vectors - administration & dosage Genetic Vectors - genetics Humans Phenotype
Online-Zugang:	Volltext
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