A Review of Methodological Considerations for Economic Evaluations of Gene Therapies and Their Application in Literature

To identify methodological considerations discussed in literature addressing economic evaluations (EEs) of gene therapies (GTs). Additionally, we assessed if these considerations are applied in published GT EEs to increase understanding and explore impact. First a peer-reviewed literature review was...

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Veröffentlicht in:Value in health 2020-09, Vol.23 (9), p.1268-1280
Hauptverfasser: ten Ham, Renske M.T., Klungel, Olaf H., Leufkens, Hubert G.M., Frederix, Geert W.J.
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Sprache:eng
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