Standards of care for CFTR variant-specific therapy (including modulators) for people with cystic fibrosis

Cystic fibrosis (CF) has entered the era of variant-specific therapy, tailored to the genetic variants in the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) gene. CFTR modulators, the first variant -specific therapy available, have transformed the management of CF.The latest standards of...

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Hauptverfasser:	Southern, Kevin W, Castellani, Carlo, Lammertyn, Elise, Smyth, Alan, VanDevanter, Donald, van Koningsbruggen-Rietschel, Silke, Barben, Jürg, Bevan, Amanda, Brokaar, Edwin, Collins, Sarah, Connett, Gary J, Daniels, Thomas W.V, Davies, Jane, Declercq, Dimitri, Gartner, Silvia, Gramegna, Andrea, Hamilton, Naomi, Hauser, Jenny, Kashirskaya, Nataliya, Kessler, Laurence, Lowdon, Jacqueline, Makukh, Halyna, Martin, Clémence, Morrison, Lisa, Nazareth, Dilip, Noordhoek, Jacquelien, O'Neill, Ciaran, Owen, Elizabeth, Oxley, Helen, Raraigh, Karen S, Raynal, Caroline, Robinson, Karen, Roehmel, Jobst, Schwarz, Carsten, Sermet, Isabelle, Shteinberg, Michal, Sinha, Ian, Takawira, Constance, van Mourik, Peter, Verkleij, Marieke, Waller, Michael D, Duff, Alistair
Format:	Artikel
Sprache:	eng
Schlagworte:	CFTR CFTR modulators Cystic fibrosis Guidelines Medicine and Health Sciences Pediatrics, Perinatology and Child Health Pulmonary and Respiratory Medicine Variant-specific therapy
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