COMPOUNDS FOR USE IN THE TREATMENT OF DYSTROPHINOPATHIES

The present invention relates to a compound selected from the group consisting of Veliflapon, Difenpiramide, Amopyroquine, Cloricromen, Alpelisib, Benorilate, Xipamide, Fabomotizole and Altizide, or a pharmaceutically acceptable salt thereof, and to combinations thereof, for use in the treatment or...

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Hauptverfasser: ASAKURA, Atsushi, PERICOT MOHR, Gal.la, ASAKURA, Yoko, HUERTAS GAMBÍN, Óscar, REIG BOLAÑO, Núria, MONTOLIO DEL OLMO, Marisol, INSA BORONAT, Raúl
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creator ASAKURA, Atsushi
PERICOT MOHR, Gal.la
ASAKURA, Yoko
HUERTAS GAMBÍN, Óscar
REIG BOLAÑO, Núria
MONTOLIO DEL OLMO, Marisol
INSA BORONAT, Raúl
description The present invention relates to a compound selected from the group consisting of Veliflapon, Difenpiramide, Amopyroquine, Cloricromen, Alpelisib, Benorilate, Xipamide, Fabomotizole and Altizide, or a pharmaceutically acceptable salt thereof, and to combinations thereof, for use in the treatment or prevention of a dystrophinopathy.
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subjects HUMAN NECESSITIES
HYGIENE
MEDICAL OR VETERINARY SCIENCE
PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES
SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS ORMEDICINAL PREPARATIONS
title COMPOUNDS FOR USE IN THE TREATMENT OF DYSTROPHINOPATHIES
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