ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES

Alternative splicing events in genes can lead to non-productive mRNA transcripts which in turn can lead to aberrant protein expression, and therapeutic agents which can target the alternative splicing events in genes can modulate the expression level of functional proteins in patients and/or inhibit...

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Hauptverfasser: AZNAREZ, Isabel, TICHO, Baruch, KACH, Jacob, JING, Enxuan, SCHARNER, Juergen, LIAU, Gene, VENKATESH, Aditya
Format: Patent
Sprache:eng ; fre ; ger
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