OLIGONUCLEOTIDE FOR THE TREATMENT OF MUSCULAR DYSTROPHY PATIENTS

The invention relates to an oligonucleotide and to a pharmaceutical composition comprising said oligonucleotide. This oligonucleotide is able to bind to a region of a first exon from a dystrophin pre-mRNA and to a region of a second exon within the same pre-mRNA, wherein said region of said second e...

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Bibliographische Detailangaben
1. Verfasser: van Deutekom, Judith Christina Theodora
Format: Patent
Sprache:eng ; fre ; ger
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