A method for the treatment of pompe disease using 1-deoxynojirimycin and derivatives

A combination therapy for use in the treatment of Pompe Disease, the combination therapy comprising a 1-deoxynojirimycin (DNJ) derivative and acid α-glucosidase (Gaa), wherein the DNJ derivative comprises a compound of the formula:where R1 is H or a straight or branched alkyl, cycloalkyl, alkenyl, a...

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Bibliographische Detailangaben
1. Verfasser: Mugrage, Benjamin
Format: Patent
Sprache:eng ; fre ; ger
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