Improved AAV vectors for gene therapy

The present invention is directed to methods for generating high titer, contaminant free, recombinant AAV vectors, methods and genetic constructs for producing AAV recombinant vectors conveniently and in large quantities, methods for the delivery of all essential viral proteins required in trans for...

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Bibliographische Detailangaben
Hauptverfasser: VINCENT, KAREN, WADSWORTH, SAMUEL C, PIRAINO, SUSAN, KYOSTIO, SIRKKA
Format: Patent
Sprache:eng ; fre ; ger
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