Adeno-associated viral compositions for IDS gene transfer and methods of use thereof
Adeno-associated virus (AAV) compositions that can restore IDS gene function of a cell and methods for using these AAV compositions to treat conditions associated with reduced IDS gene function (e.g., Hunter Syndrome) are provided. Compositions, systems, and methods for making the AAV compositions a...
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| creator | SMITH LAURA JANE GINGRAS JACQUES BURNHAM BRIAN PATEL KETAN WHITE YANNICK DOLIVE STEPHEN N VAN LIESHOUT, LEON |
| description | Adeno-associated virus (AAV) compositions that can restore IDS gene function of a cell and methods for using these AAV compositions to treat conditions associated with reduced IDS gene function (e.g., Hunter Syndrome) are provided. Compositions, systems, and methods for making the AAV compositions are also provided.
提供了可以恢复细胞的IDS基因功能的腺相关病毒(AAV)组合物以及用于使用这些AAV组合物治疗与IDS基因功能的降低相关的病症(例如，亨特综合征)的方法。还提供了用于制备所述AAV组合物的组合物、系统和方法。 |
| format | Patent |
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提供了可以恢复细胞的IDS基因功能的腺相关病毒(AAV)组合物以及用于使用这些AAV组合物治疗与IDS基因功能的降低相关的病症(例如，亨特综合征)的方法。还提供了用于制备所述AAV组合物的组合物、系统和方法。</description><language>chi ; eng</language><subject>BEER ; BIOCHEMISTRY ; CHEMISTRY ; COMPOSITIONS THEREOF ; CULTURE MEDIA ; ENZYMOLOGY ; HUMAN NECESSITIES ; HYGIENE ; MEDICAL OR VETERINARY SCIENCE ; METALLURGY ; MICROBIOLOGY ; MICROORGANISMS OR ENZYMES ; MUTATION OR GENETIC ENGINEERING ; PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES ; PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS ; SPIRITS ; VINEGAR ; WINE</subject><creationdate>2022</creationdate><oa>free_for_read</oa><woscitedreferencessubscribed>false</woscitedreferencessubscribed></display><links><openurl>$$Topenurl_article</openurl><openurlfulltext>$$Topenurlfull_article</openurlfulltext><thumbnail>$$Tsyndetics_thumb_exl</thumbnail><linktohtml>$$Uhttps://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20221216&DB=EPODOC&CC=CN&NR=115484975A$$EHTML$$P50$$Gepo$$Hfree_for_read</linktohtml><link.rule.ids>230,308,780,885,25563,76418</link.rule.ids><linktorsrc>$$Uhttps://worldwide.espacenet.com/publicationDetails/biblio?FT=D&date=20221216&DB=EPODOC&CC=CN&NR=115484975A$$EView_record_in_European_Patent_Office$$FView_record_in_$$GEuropean_Patent_Office$$Hfree_for_read</linktorsrc></links><search><creatorcontrib>SMITH LAURA JANE</creatorcontrib><creatorcontrib>GINGRAS JACQUES</creatorcontrib><creatorcontrib>BURNHAM BRIAN</creatorcontrib><creatorcontrib>PATEL KETAN</creatorcontrib><creatorcontrib>WHITE YANNICK</creatorcontrib><creatorcontrib>DOLIVE STEPHEN N</creatorcontrib><creatorcontrib>VAN LIESHOUT, LEON</creatorcontrib><title>Adeno-associated viral compositions for IDS gene transfer and methods of use thereof</title><description>Adeno-associated virus (AAV) compositions that can restore IDS gene function of a cell and methods for using these AAV compositions to treat conditions associated with reduced IDS gene function (e.g., Hunter Syndrome) are provided. Compositions, systems, and methods for making the AAV compositions are also provided.
提供了可以恢复细胞的IDS基因功能的腺相关病毒(AAV)组合物以及用于使用这些AAV组合物治疗与IDS基因功能的降低相关的病症(例如，亨特综合征)的方法。还提供了用于制备所述AAV组合物的组合物、系统和方法。</description><subject>BEER</subject><subject>BIOCHEMISTRY</subject><subject>CHEMISTRY</subject><subject>COMPOSITIONS THEREOF</subject><subject>CULTURE MEDIA</subject><subject>ENZYMOLOGY</subject><subject>HUMAN NECESSITIES</subject><subject>HYGIENE</subject><subject>MEDICAL OR VETERINARY SCIENCE</subject><subject>METALLURGY</subject><subject>MICROBIOLOGY</subject><subject>MICROORGANISMS OR ENZYMES</subject><subject>MUTATION OR GENETIC ENGINEERING</subject><subject>PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES</subject><subject>PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS</subject><subject>SPIRITS</subject><subject>VINEGAR</subject><subject>WINE</subject><fulltext>true</fulltext><rsrctype>patent</rsrctype><creationdate>2022</creationdate><recordtype>patent</recordtype><sourceid>EVB</sourceid><recordid>eNqNjDEOwjAMALMwIOAP5gEdKloBY1VAsLDQvbISp43U2lEceD8deADTDXe6tekaRywFqooNmMnBJyScwMocRUMOwgpeEjwuLxiICXJCVk8JkB3MlEdxCuLhrYsbKZH4rVl5nJR2P27M_nbt2ntBUXrSiHYZ5b59lmVdnarzsW4O_zRfd2I4jQ</recordid><startdate>20221216</startdate><enddate>20221216</enddate><creator>SMITH LAURA JANE</creator><creator>GINGRAS JACQUES</creator><creator>BURNHAM BRIAN</creator><creator>PATEL KETAN</creator><creator>WHITE YANNICK</creator><creator>DOLIVE STEPHEN N</creator><creator>VAN LIESHOUT, LEON</creator><scope>EVB</scope></search><sort><creationdate>20221216</creationdate><title>Adeno-associated viral compositions for IDS gene transfer and methods of use thereof</title><author>SMITH LAURA JANE ; GINGRAS JACQUES ; BURNHAM BRIAN ; PATEL KETAN ; WHITE YANNICK ; DOLIVE STEPHEN N ; VAN LIESHOUT, LEON</author></sort><facets><frbrtype>5</frbrtype><frbrgroupid>cdi_FETCH-epo_espacenet_CN115484975A3</frbrgroupid><rsrctype>patents</rsrctype><prefilter>patents</prefilter><language>chi ; eng</language><creationdate>2022</creationdate><topic>BEER</topic><topic>BIOCHEMISTRY</topic><topic>CHEMISTRY</topic><topic>COMPOSITIONS THEREOF</topic><topic>CULTURE MEDIA</topic><topic>ENZYMOLOGY</topic><topic>HUMAN NECESSITIES</topic><topic>HYGIENE</topic><topic>MEDICAL OR VETERINARY SCIENCE</topic><topic>METALLURGY</topic><topic>MICROBIOLOGY</topic><topic>MICROORGANISMS OR ENZYMES</topic><topic>MUTATION OR GENETIC ENGINEERING</topic><topic>PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES</topic><topic>PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS</topic><topic>SPIRITS</topic><topic>VINEGAR</topic><topic>WINE</topic><toplevel>online_resources</toplevel><creatorcontrib>SMITH LAURA JANE</creatorcontrib><creatorcontrib>GINGRAS JACQUES</creatorcontrib><creatorcontrib>BURNHAM BRIAN</creatorcontrib><creatorcontrib>PATEL KETAN</creatorcontrib><creatorcontrib>WHITE YANNICK</creatorcontrib><creatorcontrib>DOLIVE STEPHEN N</creatorcontrib><creatorcontrib>VAN LIESHOUT, LEON</creatorcontrib><collection>esp@cenet</collection></facets><delivery><delcategory>Remote Search Resource</delcategory><fulltext>fulltext_linktorsrc</fulltext></delivery><addata><au>SMITH LAURA JANE</au><au>GINGRAS JACQUES</au><au>BURNHAM BRIAN</au><au>PATEL KETAN</au><au>WHITE YANNICK</au><au>DOLIVE STEPHEN N</au><au>VAN LIESHOUT, LEON</au><format>patent</format><genre>patent</genre><ristype>GEN</ristype><title>Adeno-associated viral compositions for IDS gene transfer and methods of use thereof</title><date>2022-12-16</date><risdate>2022</risdate><abstract>Adeno-associated virus (AAV) compositions that can restore IDS gene function of a cell and methods for using these AAV compositions to treat conditions associated with reduced IDS gene function (e.g., Hunter Syndrome) are provided. Compositions, systems, and methods for making the AAV compositions are also provided.
提供了可以恢复细胞的IDS基因功能的腺相关病毒(AAV)组合物以及用于使用这些AAV组合物治疗与IDS基因功能的降低相关的病症(例如，亨特综合征)的方法。还提供了用于制备所述AAV组合物的组合物、系统和方法。</abstract><oa>free_for_read</oa></addata></record> |
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| subjects | BEER BIOCHEMISTRY CHEMISTRY COMPOSITIONS THEREOF CULTURE MEDIA ENZYMOLOGY HUMAN NECESSITIES HYGIENE MEDICAL OR VETERINARY SCIENCE METALLURGY MICROBIOLOGY MICROORGANISMS OR ENZYMES MUTATION OR GENETIC ENGINEERING PREPARATIONS FOR MEDICAL, DENTAL, OR TOILET PURPOSES PROPAGATING, PRESERVING OR MAINTAINING MICROORGANISMS SPIRITS VINEGAR WINE |
| title | Adeno-associated viral compositions for IDS gene transfer and methods of use thereof |
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