Acetyl-L-Leucine for Niemann-Pick type C: A Multinational Double-blind Randomized Placebo-controlled Crossover Study (P14-11.001)

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Veröffentlicht in:Neurology 2023-04, Vol.100 (17_supplement_2)
Hauptverfasser: Bremova-Ertl, Tatiana, Fields, Taylor, Martakis, Kyriakos, Strupp, Michael
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container_title Neurology
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creator Bremova-Ertl, Tatiana
Fields, Taylor
Martakis, Kyriakos
Strupp, Michael
description Abstract only
doi_str_mv 10.1212/WNL.0000000000203666
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title Acetyl-L-Leucine for Niemann-Pick type C: A Multinational Double-blind Randomized Placebo-controlled Crossover Study (P14-11.001)
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