Lentiviral Gene Therapy with Low Dose Conditioning for X-Linked SCID Results in Complete Immune Reconstitution and No Evidence of Clonal Expansion
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Veröffentlicht in: | Blood 2022-11, Vol.140 (Supplement 1), p.7770-7771 |
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container_issue | Supplement 1 |
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container_title | Blood |
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creator | Booth, Claire Kohn, Donald B. Armant, Myriam Prockop, Susan Buckland, Karen Chandra, Sharat Chandrakasan, Shanmuganathan Chetty, Kritika Dansereau, Colleen de Oliveira, Satiro Everett, John León Rico, Diego London, Wendy B. Xu-Bayford, Jin Hua Moore, Theodore B. Nagarsheth, Nisha Parikh, Suhag Terrazas, Dayna White, Shanna L Schambach, Axel Bushman, Frederic D. Thrasher, Adrian J. Williams, David A. Pai, Sung-Yun |
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doi_str_mv | 10.1182/blood-2022-159979 |
format | Article |
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source | Elektronische Zeitschriftenbibliothek - Frei zugängliche E-Journals; Alma/SFX Local Collection |
title | Lentiviral Gene Therapy with Low Dose Conditioning for X-Linked SCID Results in Complete Immune Reconstitution and No Evidence of Clonal Expansion |
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