The clinical landscape for AAV gene therapies von Kuzmin, Dmitry A., Shutova, Maria V., Johnston, Natalie R., Smith, Owen P., Fedorin, Vasily V., Kukushkin, Yury S., van der Loo, Johannes C.M., Johnstone, Elaine C.

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Progress and challenges in viral vector manufacturing von van der Loo, Johannes C M, Wright, J Fraser

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Selecting a Cell Engineering Methodology During Cell Therapy Product Development von Timmins, Lauren M., Burr, Alexandra M., Carroll, Kristina, Keefe, Robert, Teryek, Matthew, Cantolupo, Louis J., van der Loo, Johannes C. M., Heathman, Thomas R.J., Gormley, Adam J, Smith, David, Parekkadan, Biju

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PU.1 Redirects Adenovirus to Lysosomes in Alveolar Macrophages, Uncoupling Internalization from Infection von Carey, Brenna, Staudt, Margaret K, Bonaminio, Dana, van der Loo, Johannes C. M, Trapnell, Bruce C

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Familial pulmonary alveolar proteinosis caused by mutations in CSF2RA von Suzuki, Takuji, Sakagami, Takuro, Rubin, Bruce K, Nogee, Lawrence M, Wood, Robert E, Zimmerman, Sarah L, Smolarek, Teresa, Dishop, Megan K, Wert, Susan E, Whitsett, Jeffrey A, Grabowski, Gregory, Carey, Brenna C, Stevens, Carrie, van der Loo, Johannes C M, Trapnell, Bruce C

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Process Development for the Production and Purification of Adeno-Associated Virus (AAV)2 Vector using Baculovirus-Insect Cell Culture System von Nasimuzzaman, Md, Villaveces, Sophia, van der Loo, Johannes C M, Alla, Sivani

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Purification of baculovirus vectors using heparin affinity chromatography von Nasimuzzaman, Md, Lynn, Danielle, van der Loo, Johannes Cm, Malik, Punam

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Preclinical Evaluation of Foamy Virus Vector-Mediated Gene Addition in Human Hematopoietic Stem/Progenitor Cells for Correction of Leukocyte Adhesion Deficiency Type 1 von Smith, Richard H, Bloomer, Hanan, Fink, Danielle, Keyvanfar, Keyvan, Nasimuzzaman, Md, Sancheznieto, Fátima, Dutta, Roop, Guenther Bui, Kacey, Alvarado, Luigi J, Bauer, Jr, Thomas R, Hickstein, Dennis D, Russell, David W, Malik, Punam, van der Loo, Johannes C M, Highfill, Steven L, Kuhns, Douglas B, Pirooznia, Mehdi, Larochelle, Andre

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Evaluation of a rapid multi-attribute combinatorial high-throughput UV-Vis/DLS/SLS analytical platform for rAAV quantification and characterization von Liu, Xueyuan, Jean-Gilles, Riffard, Baginski, Julia, Cai, Christina, Yan, Ruilan, Zhang, Lili, Lance, Kevin, van der Loo, Johannes C.M., Davidson, Beverly L.

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Production and purification of high-titer foamy virus vector for the treatment of leukocyte adhesion deficiency von Nasimuzzaman, Md, Lynn, Danielle, Ernst, Rebecca, Beuerlein, Michele, Smith, Richard H, Shrestha, Archana, Cross, Scott, Link, Kevin, Lutzko, Carolyn, Nordling, Diana, Russell, David W, Larochelle, Andre, Malik, Punam, Van der Loo, Johannes C M

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Production and Purification of Baculovirus for Gene Therapy Application von Nasimuzzaman, Md, van der Loo, Johannes C M, Malik, Punam

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Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant von George, Lindsey A, Sullivan, Spencer K, Giermasz, Adam, Rasko, John E.J, Samelson-Jones, Benjamin J, Ducore, Jonathan, Cuker, Adam, Sullivan, Lisa M, Majumdar, Suvankar, Teitel, Jerome, McGuinn, Catherine E, Ragni, Margaret V, Luk, Alvin Y, Hui, Daniel, Wright, J. Fraser, Chen, Yifeng, Liu, Yun, Wachtel, Katie, Winters, Angela, Tiefenbacher, Stefan, Arruda, Valder R, van der Loo, Johannes C.M, Zelenaia, Olga, Takefman, Daniel, Carr, Marcus E, Couto, Linda B, Anguela, Xavier M, High, Katherine A

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The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute von Flotte, Terence R, Daniels, Eric, Benson, Janet, Bevett-Rose, Jeneé M, Cornetta, Kenneth, Diggins, Margaret, Johnston, Julie, Sepelak, Susan, van der Loo, Johannes C M, Wilson, James M, McDonald, Cheryl L

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Process Development for the Production and Purification of Adeno-Associated Virus (AAV)2 Vector using Baculovirus-Insect Cell Culture System von Nasimuzzaman, Md, Villaveces, Sophia, van der Loo, Johannes C. M., Alla, Sivani

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Simultaneous Infection with Retroviruses Pseudotyped with Different Envelope Proteins Bypasses Viral Receptor Interference Associated with Colocalization of gp70 and Target Cells o... von MacNeill, E C, Hanenberg, H, Pollok, K E, van der Loo, J C, Bierhuizen, M F, Wagemaker, G, Williams, D A

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Design and Production of Retro- and Lentiviral Vectors for Gene Expression in Hematopoietic Cells von Schambach, Axel, Swaney, William P., Loo, Johannes C.M. van der

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Optimization of gene transfer into primitive human hematopoietic cells of granulocyte-colony stimulating factor-mobilized peripheral blood using low-dose cytokines and comparison o... von VAN DER LOO, Johannes C. M, LIU, B. L, GOLDMAN, A. I, BUCKLEY, S. M, CHRUDIMSKY, K. S

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285. Foamy Viral Vector Expressing Human CD18 Results in High Levels of Transduction and Multilineage Engraftment with CD18+ LAD-1 Cells in NSG Mice von Smith, Richard H., Nasimuzzaman, Md, Dutta, Roop, Uzel, Gulbu, Bauer, Thomas R., Holland, Steven M., Russell, David W., Hickstein, Dennis D., Malik, Punam, Loo, Johannes C. M. van der, Larochelle, Andre

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Homing defect of cultured human hematopoietic cells in the NOD/SCID mouse is mediated by Fas/CD95 von Liu, Bianling, Buckley, Sharron M, Lewis, Ian D, Goldman, Anne I, Wagner, John E, van der Loo, Johannes C.M

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Critical Variables Affecting Clinical-Grade Production of the Self-Inactivating Gamma-Retroviral Vector for the Treatment of X-linked Severe Combined Immunodeficiency von van der Loo, Johannes CM, Swaney, William P, Grassman, Elke, Terwilliger, Ami, Higashimoto, Tomoyasu, Schambach, Axel, Hacein-Bey-Abina, Salima, Nordling, Diana L, Cavazzana-Calvo, Marina, Thrasher, Adrian J, Williams, David A, Reeves, Lilith, Malik, Punam

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