Treatment of a Mouse Model of ALS by In Vivo Base Editing von Lim, Colin K.W., Gapinske, Michael, Brooks, Alexandra K., Woods, Wendy S., Powell, Jackson E., Zeballos C., M. Alejandra, Winter, Jackson, Perez-Pinera, Pablo, Gaj, Thomas

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CRISPR-SKIP: programmable gene splicing with single base editors von Gapinske, Michael, Luu, Alan, Winter, Jackson, Woods, Wendy S, Kostan, Kurt A, Shiva, Nikhil, Song, Jun S, Perez-Pinera, Pablo

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Clinical, radiological and molecular responses to combination chemotherapy with MAPK pathway inhibition in relapsed and refractory Langerhans cell histiocytosis von Karri, Vivekanudeep, Lin, Howard, Velazquez, Jessica, Batajoo, Akanksha, Parekh, Deevyashali, Stanton, Whitney, Abhyankar, Harshal, El‐Mallawany, Nader K., Agrusa, Jennifer, Eckstein, Olive, Gulati, Nitya, Schwartz, Jeffrey, Woods‐Swafford, Wendy, Boyd, Jaime, Saha, Anikit, Allen, Carl E., McClain, Kenneth L.

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Disruption of the β1L Isoform of GABP Reverses Glioblastoma Replicative Immortality in a TERT Promoter Mutation-Dependent Manner von Mancini, Andrew, Xavier-Magalhães, Ana, Woods, Wendy S., Nguyen, Kien-Thiet, Amen, Alexandra M., Hayes, Josie L., Fellmann, Christof, Gapinske, Michael, McKinney, Andrew M., Hong, Chibo, Jones, Lindsey E., Walsh, Kyle M., Bell, Robert J.A., Doudna, Jennifer A., Costa, Bruno M., Song, Jun S., Perez-Pinera, Pablo, Costello, Joseph F.

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Site-specific perturbations of alpha-synuclein fibril structure by the Parkinson's disease associated mutations A53T and E46K von Lemkau, Luisel R, Comellas, Gemma, Lee, Shin W, Rikardsen, Lars K, Woods, Wendy S, George, Julia M, Rienstra, Chad M

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SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping von Miskalis, Angelo, Shirguppe, Shraddha, Winter, Jackson, Elias, Gianna, Swami, Devyani, Nambiar, Ananthan, Stilger, Michelle, Woods, Wendy S., Gosstola, Nicholas, Gapinske, Michael, Zeballos, Alejandra, Moore, Hayden, Maslov, Sergei, Gaj, Thomas, Perez-Pinera, Pablo

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Multiplexed and tunable transcriptional activation by promoter insertion using nuclease-assisted vector integration von Brown, Alexander, Winter, Jackson, Gapinske, Michael, Tague, Nathan, Woods, Wendy S, Perez-Pinera, Pablo

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Epigenetic engineering of yeast reveals dynamic molecular adaptation to methylation stress and genetic modulators of specific DNMT3 family members von Finnegan, Alex, Kim, Somang, Jin, Hu, Gapinske, Michael, Woods, Wendy S., Perez-Pinera, Pablo, Song, Jun S.

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Prosurvival long noncoding RNA PINCR regulates a subset of p53 targets in human colorectal cancer cells by binding to Matrin 3 von Chaudhary, Ritu, Gryder, Berkley, Woods, Wendy S, Subramanian, Murugan, Jones, Matthew F, Li, Xiao Ling, Jenkins, Lisa M, Shabalina, Svetlana A, Mo, Min, Dasso, Mary, Yang, Yuan, Wakefield, Lalage M, Zhu, Yuelin, Frier, Susan M, Moriarity, Branden S, Prasanth, Kannanganattu V, Perez-Pinera, Pablo, Lal, Ashish

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Study of Wild-Type α‑Synuclein Binding and Orientation on Gold Nanoparticles von Yang, Jie An, Johnson, Brittany J, Wu, Sway, Woods, Wendy S, George, Julia M, Murphy, Catherine J

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Corrigendum: Chromatin structure and context-dependent sequence features control prime editing efficiency von Kim, Somang, Yuan, Jimmy B, Woods, Wendy S, Newton, Destry A, Perez-Pinera, Pablo, Song, Jun S

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Chromatin structure and context-dependent sequence features control prime editing efficiency von Kim, Somang, Yuan, Jimmy B, Woods, Wendy S, Newton, Destry A, Perez-Pinera, Pablo, Song, Jun S

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Acute increase of α-synuclein inhibits synaptic vesicle recycling evoked during intense stimulation von Busch, David J, Oliphint, Paul A, Walsh, Rylie B, Banks, Susan M L, Woods, Wendy S, George, Julia M, Morgan, Jennifer R

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Structured Regions of α-Synuclein Fibrils Include the Early-Onset Parkinson's Disease Mutation Sites von Comellas, Gemma, Lemkau, Luisel R., Nieuwkoop, Andrew J., Kloepper, Kathryn D., Ladror, Daniel T., Ebisu, Reika, Woods, Wendy S., Lipton, Andrew S., George, Julia M., Rienstra, Chad M.

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α‑Synuclein’s Adsorption, Conformation, and Orientation on Cationic Gold Nanoparticle Surfaces Seeds Global Conformation Change von Yang, Jie An, Lin, Wayne, Woods, Wendy S, George, Julia M, Murphy, Catherine J

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Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors von Gapinske, Michael, Winter, Jackson, Swami, Devyani, Gapinske, Lauren, Woods, Wendy S., Shirguppe, Shraddha, Miskalis, Angelo, Busza, Anna, Joulani, Dana, Kao, Collin J., Kostan, Kurt, Bigot, Anne, Bashir, Rashid, Perez-Pinera, Pablo

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Targeted Gene Activation Using RNA-Guided Nucleases von Brown, Alexander, Woods, Wendy S., Perez-Pinera, Pablo

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Mutant Protein A30P α-Synuclein Adopts Wild-type Fibril Structure, Despite Slower Fibrillation Kinetics von Lemkau, Luisel R., Comellas, Gemma, Kloepper, Kathryn D., Woods, Wendy S., George, Julia M., Rienstra, Chad M.

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Targeted exon skipping with AAV-mediated split adenine base editors von Winter, Jackson, Luu, Alan, Gapinske, Michael, Manandhar, Sony, Shirguppe, Shraddha, Woods, Wendy S., Song, Jun S., Perez-Pinera, Pablo

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Dynamic transport and localization of alpha-synuclein in primary hippocampal neurons von Yang, Mong-Lin, Hasadsri, Linda, Woods, Wendy S, George, Julia M

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