O11 Peptide modified AONs for enhanced potency and tissue targeting von Wood, M.J.A

Volltext

Unravelling the role of androgen receptor splice variants in the mechanisms of pathogenesis of spinal and bulbar muscular atrophy von Lieto, M, Wood, M.J.A, Rinaldi, C

Volltext

Oligonucleotide therapies for neuromuscular disease von Wood, M.J.A.

Volltext

S04 - Oligonucleotide therapies for neuromuscular disease von Wood, M.J.A.

Volltext

T.I.2 Antisense oligonucleotide exon skipping therapy for DMD von Wood, M.J.A

Volltext

The role of the TWEAK/Fn14 pathway in muscle pathology in SMA von Meijboom, K.E, Hazell, G, McFall, E, Deguise, M.-O, Anthony, D, Burkly, L.C, Kothary, R, Wood, M.J.A, Bowerman, M

Volltext

P21 Strategies for brain targeting using peptide-conjugated antisense oligonucleotides von Douglas, A.G.L, Shabanpoor, F, Hammond, S.M, Gait, M.J, Wood, M.J.A

Volltext

Age-related and mutation-independent proteomic changes in dystrophic mouse muscle von van Westering, T.L.E, Johansson, H.J, Coenen-Stass, A.M.L, Tanihata, J, Takeda, S, Yokota, T, Lehtiö, J, Wood, M.J.A, El Andaloussi, S, Roberts, T.C, Aoki, Y

Volltext

The glucocorticoid-KLF15-BCAA pathway as a novel therapeutic target for spinal muscular atrophy von Walter, L.M, Betts, C.A, Meijboom, K.E, van Westering, T.L.E, Hazell, G, McFall, E, Deguise, M.-O, Kothary, R, Wood, M.J.A, Bowerman, M

Volltext

C9ORF72 and RAB7L1 regulate vesicle traffi cking in Amyotrophic Lateral Sclerosis and Frontotemporal Dementia von Manzano, R, Aoki, Y, Lee, Y, Dafinca, R, Aoki, M, Douglas, A.G.L, Varela, M.A, Sathyaprakash, C, Scaber, J, Barbagallo, P, Vader, P, Mäger, I, Ezzat, K, Turner, M.R, Ito, N, Gasco, S, Ohbayashi, N, El Andaloussi, S, Taked, S, Fukuda, M, Talbot, K, Wood, M.J.A

Volltext

MN08 - Unravelling the role of androgen receptor splice variants in the mechanisms of pathogenesis of spinal and bulbar muscular atrophy von Lieto, M., Wood, M.J.A., Rinaldi, C.

Volltext

T.P.2.10 Restoration of dystrophin expression in mdx mouse by peptide-conjugated antisense oligonucleotides von Yin, H.F, Seow, Y.Q, Moulton, H.M, Iversen, P.L, Boutilier, J.K, Wood, M.J.A

Volltext

P03 Exon skipping and dystrophin restoration in Duchenne muscular dystrophy patients after systemic phosphorodiamidate morpholino oligomer treatment von Cirak, S, Arechavala-Gomeza, V, Guglieri, M, Feng, L, Torelli, S, Anthony, K, Garralda, M.E, Wells, D, Dickson, G, Wood, M.J.A, Wilton, S.D, Straub, V, Shrewsbury, S.B, Sewry, C, Morgan, J.E, Bushby, K, Muntoni, F

Volltext

Profile of circadianly regulated metabolic genes in dystrophic heart von Betts, C.A., van Westering, T.L.E., Bowerman, M., McClorey, G., Meijboom, K., Wood, M.J.A.

Volltext

D43 - Profile of circadianly regulated metabolic genes in dystrophic heart von Betts, C.A., van Westering, T.L.E., Bowerman, M., McClorey, G., Meijboom, K., Wood, M.J.A.

Volltext

T.O.3 Restoration of dystrophin expression in Duchenne muscular dystrophy: A single blind, placebo-controlled dose escalation study using morpholino oligomer AVI-4658 von Kinali, M, Arechavala-Gomeza, V, Feng, L, Cirak, S, Hunt, D, Adkin, C, Guglieri, M, Abbs, S, Nihoyannopoulos, P, Garralda, M.E, Rutherford, M, McCulley, C, Popplewell, L, Graham, I.R, Dickson, G, Wood, M.J.A, Wells, D.J, Wilton, S.D, Holt, T, Kole, R, Straub, V, Bushby, K, Sewry, C, Morgan, J.E, Muntoni, F

Volltext

Extracellular myomiR abundance is not clearly correlated with skeletal muscle dystrophin expression in mdx mice with skewed X-chromosome inactivation von van Westering, T., Coenen-Stass, A.M.L., Hulsker, M., Aartsma-Rus, A., Wood, M.J.A., van Putten, M., Roberts, T.C.

Volltext

D44 - Extracellular myomiR abundance is not clearly correlated with skeletal muscle dystrophin expression in mdx mice with skewed X-chromosome inactivation von van Westering, T., Coenen-Stass, A.M.L., Hulsker, M., Aartsma-Rus, A., Wood, M.J.A., van Putten, M., Roberts, T.C.

Volltext

A γ34.5 Mutant of Herpes Simplex 1 Causes Severe Inflammation in the Brain von McMenamin, M.M., Byrnes, A.P., Charlton, H.M., Coffin, R.S., Latchman, D.S., Wood, M.J.A.

Volltext

MN07 - The role of the TWEAK/Fn14 pathway in muscle pathology in SMA von Meijboom, K.E., Hazell, G., McFall, E., Deguise, M.-O., Anthony, D., Burkly, L.C., Kothary, R., Wood, M.J.A., Bowerman, M.

Volltext