Delivery of siRNA to the mouse brain by systemic injection of targeted exosomes von Wood, Matthew J A, Alvarez-Erviti, Lydia, Seow, Yiqi, Yin, HaiFang, Betts, Corinne, Lakhal, Samira

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DNA Cage Delivery to Mammalian Cells von Walsh, Anthony S, Yin, HaiFang, Erben, Christoph M, Wood, Matthew J. A, Turberfield, Andrew J

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The role of long non-coding RNAs in neurodevelopment, brain function and neurological disease von Roberts, Thomas C., Morris, Kevin V., Wood, Matthew J. A.

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Advances in oligonucleotide drug delivery von Roberts, Thomas C., Langer, Robert, Wood, Matthew J. A.

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A CRISPR-Cas9-based reporter system for single-cell detection of extracellular vesicle-mediated functional transfer of RNA von de Jong, Olivier G., Murphy, Daniel E., Mäger, Imre, Willms, Eduard, Garcia-Guerra, Antonio, Gitz-Francois, Jerney J., Lefferts, Juliet, Gupta, Dhanu, Steenbeek, Sander C., van Rheenen, Jacco, El Andaloussi, Samir, Schiffelers, Raymond M., Wood, Matthew J. A., Vader, Pieter

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Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-... von Cirak, Sebahattin, MD, Arechavala-Gomeza, Virginia, PhD, Guglieri, Michela, MD, Feng, Lucy, PhD, Torelli, Silvia, PhD, Anthony, Karen, PhD, Abbs, Stephen, PhD, Garralda, Maria Elena, Prof, Bourke, John, MD, Wells, Dominic J, Prof, Dickson, George, Prof, Wood, Matthew JA, MD PhD, Wilton, Steve D, Prof, Straub, Volker, Prof, Kole, Ryszard, Prof, Shrewsbury, Stephen B, MD, Sewry, Caroline, Prof, Morgan, Jennifer E, PhD, Bushby, Kate, Prof, Muntoni, Francesco, Prof

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Alpha-synuclein induces the unfolded protein response in Parkinson's disease SNCA triplication iPSC-derived neurons von Heman-Ackah, Sabrina M, Manzano, Raquel, Hoozemans, Jeroen J M, Scheper, Wiep, Flynn, Rowan, Haerty, Wilfried, Cowley, Sally A, Bassett, Andrew R, Wood, Matthew J A

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Targeting RNA to treat neuromuscular disease von Muntoni, Francesco, Wood, Matthew J. A

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Extracellular Vesicle Heterogeneity: Subpopulations, Isolation Techniques, and Diverse Functions in Cancer Progression von Willms, Eduard, Cabañas, Carlos, Mäger, Imre, Wood, Matthew J A, Vader, Pieter

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Assessment of RT-qPCR normalization strategies for accurate quantification of extracellular microRNAs in murine serum von Roberts, Thomas C, Coenen-Stass, Anna M L, Wood, Matthew J A

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GAPDH controls extracellular vesicle biogenesis and enhances the therapeutic potential of EV mediated siRNA delivery to the brain von Dar, Ghulam Hassan, Mendes, Cláudia C., Kuan, Wei-Li, Speciale, Alfina A., Conceição, Mariana, Görgens, André, Uliyakina, Inna, Lobo, Miguel J., Lim, Wooi F., EL Andaloussi, Samir, Mäger, Imre, Roberts, Thomas C., Barker, Roger A., Goberdhan, Deborah C. I., Wilson, Clive, Wood, Matthew J. A.

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Extracellular vesicle in vivo biodistribution is determined by cell source, route of administration and targeting von Wiklander, Oscar P. B., Nordin, Joel Z., O'Loughlin, Aisling, Gustafsson, Ylva, Corso, Giulia, Mäger, Imre, Vader, Pieter, Lee, Yi, Sork, Helena, Seow, Yiqi, Heldring, Nina, Alvarez-Erviti, Lydia, Smith, CI Edvard, Le Blanc, Katarina, Macchiarini, Paolo, Jungebluth, Philipp, Wood, Matthew J. A., Andaloussi, Samir EL

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An LNA-amide modification that enhances the cell uptake and activity of phosphorothioate exon-skipping oligonucleotides von Baker, Ysobel R., Thorpe, Cameron, Chen, Jinfeng, Poller, Laura M., Cox, Lina, Kumar, Pawan, Lim, Wooi F., Lie, Lillian, McClorey, Graham, Epple, Sven, Singleton, Daniel, McDonough, Michael A., Hardwick, Jack S., Christensen, Kirsten E., Wood, Matthew J. A., Hall, James P., El-Sagheer, Afaf H., Brown, Tom

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Genetic therapies for RNA mis-splicing diseases von Hammond, Suzan M, Wood, Matthew J.A

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Cell-penetrating peptide-conjugated antisense oligonucleotides restore systemic muscle and cardiac dystrophin expression and function von Yin, HaiFang, Moulton, Hong M., Seow, Yiqi, Boyd, Corinne, Boutilier, Jordan, Iverson, Patrick, Wood, Matthew J.A.

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A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice von Yin, HaiFang, Moulton, Hong M., Betts, Corinne, Seow, Yiqi, Boutilier, Jordan, Iverson, Patrick L., Wood, Matthew J.A.

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Therapeutic approaches for Duchenne muscular dystrophy von Roberts, Thomas C., Wood, Matthew J. A., Davies, Kay E.

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Molecular and electrophysiological features of spinocerebellar ataxia type seven in induced pluripotent stem cells von Burman, Richard J, Watson, Lauren M, Smith, Danielle C, Raimondo, Joseph V, Ballo, Robea, Scholefield, Janine, Cowley, Sally A, Wood, Matthew J A, Kidson, Susan H, Greenberg, Leslie J

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FKRP-dependent glycosylation of fibronectin regulates muscle pathology in muscular dystrophy von Wood, A. J., Lin, C. H., Li, M., Nishtala, K., Alaei, S., Rossello, F., Sonntag, C., Hersey, L., Miles, L. B., Krisp, C., Dudczig, S., Fulcher, A. J., Gibertini, S., Conroy, P. J., Siegel, A., Mora, M., Jusuf, P., Packer, N. H., Currie, P. D.

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Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers von Goyenvalle, Aurélie, Griffith, Graziella, Babbs, Arran, Andaloussi, Samir El, Ezzat, Kariem, Avril, Aurélie, Dugovic, Branislav, Chaussenot, Rémi, Ferry, Arnaud, Voit, Thomas, Amthor, Helge, Bühr, Claudia, Schürch, Stefan, Wood, Matthew J A, Davies, Kay E, Vaillend, Cyrille, Leumann, Christian, Garcia, Luis

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