Risdiplam therapy in adults with 5q-SMA: observational study on motor function and treatment satisfaction von Bjelica, Bogdan, Wohnrade, Camilla, Cespedes, Iraima, Osmanovic, Alma, Schreiber-Katz, Olivia, Petri, Susanne

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Unraveling the Heterogeneity of ALS-A Call to Redefine Patient Stratification for Better Outcomes in Clinical Trials von Tzeplaeff, Laura, Jürs, Alexandra V, Wohnrade, Camilla, Demleitner, Antonia F

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Health-Related Quality of Life in Spinal Muscular Atrophy Patients and Their Caregivers-A Prospective, Cross-Sectional, Multi-Center Analysis von Wohnrade, Camilla, Velling, Ann-Kathrin, Mix, Lucas, Wurster, Claudia D, Cordts, Isabell, Stolte, Benjamin, Zeller, Daniel, Uzelac, Zeljko, Platen, Sophia, Hagenacker, Tim, Deschauer, Marcus, Lingor, Paul, Ludolph, Albert C, Lulé, Dorothée, Petri, Susanne, Osmanovic, Alma, Schreiber-Katz, Olivia

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An observational cohort study on pulmonary function in adult patients with 5q-spinal muscular atrophy under nusinersen therapy von Bjelica, Bogdan, Wohnrade, Camilla, Osmanovic, Alma, Schreiber-Katz, Olivia, Petri, Susanne

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Diagnostic value of neurofilaments in differentiating motor neuron disease from multifocal motor neuropathy von Wohnrade, Camilla, Seeliger, Tabea, Gingele, Stefan, Bjelica, Bogdan, Skripuletz, Thomas, Petri, Susanne

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Correction to: Diagnostic value of neurofilaments in differentiating motor neuron disease from multifocal motor neuropathy von Wohnrade, Camilla, Seeliger, Tabea, Gingele, Stefan, Bjelica, Bogdan, Skripuletz, Thomas, Petri, Susanne

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Metabolic syndrome is common in adults with 5q‐spinal muscular atrophy and impacts quality of life and fatigue von Bjelica, Bogdan, Wohnrade, Camilla, Osmanovic, Alma, Schreiber‐Katz, Olivia, Schuppner, Ramona, Greten, Stephan, Petri, Susanne

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Tauroursodeoxycholic acid in patients with amyotrophic lateral sclerosis: The TUDCA-ALS trial protocol von Albanese, Alberto, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Rinaldi, Gilberto, Vanacore, Nicola, Dickie, Brian

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A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid (TUDCA) as add-on treatment in patients affected by amyotrophic lateral sclerosis (ALS)... von Lombardo, Flavia L, Spila Alegiani, Stefania, Mayer, Flavia, Cipriani, Marta, Lo Giudice, Maria, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Nicolini, Gabriele, Vanacore, Nicola, Dickie, Brian, Albanese, Alberto, Puopolo, Maria

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A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid : the statistical analysis plan of TUDCA-ALS trial von Lombardo, Flavia L, Spila Alegiani, Stefania, Mayer, Flavia, Cipriani, Marta, Lo Giudice, Maria, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Nicolini, Gabriele, Vanacore, Nicola, Dickie, Brian, Albanese, Alberto, Puopolo, Maria, Tornese, Paolo, Cocco, Antoniangela, Matteoli, Michela, Lauranzano, Eliana, Malosio, Maria Luisa, Elia, Chiara Adriana, Chiò, Adriano, Manera, Umberto, Moglia, Cristina, Calvo, Andrea, Salamone, Paolina, Fuda, Giuseppe, Colosimo, Carlo, Spera, Cristina, Ranchicchio, Prabha Cristina, Stipa, Giuseppe, Frondizi, Domenico, Lunetta, Christian, Sansone, Valeria, Tarlarini, Claudia, Gerardi, Francesca, Silani, Vincenzo, Doretti, Alberto, Colombo, Eleonora, Demirtzidis, Gianluca, Tedeschi, Gioacchino, Trojsi, Francesca, Passaniti, Carla, Ballestrero, Stefania, Dorst, Johannes, Weiland, Ulrike, Fromm, Andrea, Wiesenfarth, Maximilian, Kandler, Katharina, Witzel, Simon, Otto, Markus, Schuster, Joachim, Meyer, Thomas, Maier, André, Kettemann, Dagmar, Petri, Susanne, Müschen, Lars, Wohnrade, Camilla, Sarikidi, Anastasia, Osmanovic, Alma, Grosskreutz, Julian, Rödiger, Annekathrin, Steinbach, Robert, Ilse, Benjamin, Smesny, Uta, Untucht, Robert, Günther, René, Vidovic, Maximilian, Shaw, Pamela, Collins, Alexis, Wollff, Helen, Walsh, Theresa, Tuddenham, Lee, Kazoka, Mbombe, White, David, Young, Stacy, Thompson, Benjamin, Madarshahian, Daniel, Chhetri, Suresh K, Chaouch, Amina, Young, Carolyn A, Arndt, Heike, Hanemann, Coliver, Lambert, Thomas, Beltran, Stephane, Couratier, Philippe, Esselin, Florence, Camu, William, De La Cruz, Elisa, Lemasson, Gwendal, Masrori, Pegah, Maguire, Sinead, Fogarty, Liz, Atoyebi, Toyosi, Obáin, Niamh Ní

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Unraveling the Heterogeneity of ALS—A Call to Redefine Patient Stratification for Better Outcomes in Clinical Trials von Tzeplaeff, Laura, Jürs, Alexandra V, Wohnrade, Camilla, Demleitner, Antonia F

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Risdiplam therapy in adults with 5q-SMA: observational study on motor function and treatment satisfaction von Bjelica, Bogdan, Wohnrade, Camilla, Cespedes, Iraima, Osmanovic, Alma, Schreiber-Katz, Olivia, Petri, Susanne

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A randomized double-blind clinical trial on safety and efficacy of tauroursodeoxycholic acid : the statistical analysis plan of TUDCA-ALS trial von Lombardo, Flavia L, Spila Alegiani, Stefania, Mayer, Flavia, Cipriani, Marta, Lo Giudice, Maria, Ludolph, Albert Christian, McDermott, Christopher J, Corcia, Philippe, Van Damme, Philip, Van den Berg, Leonard H, Hardiman, Orla, Nicolini, Gabriele, Vanacore, Nicola, Dickie, Brian, Albanese, Alberto, Puopolo, Maria, Tornese, Paolo, Cocco, Antoniangela, Matteoli, Michela, Lauranzano, Eliana, Malosio, Maria Luisa, Elia, Chiara Adriana, Chiò, Adriano, Manera, Umberto, Moglia, Cristina, Calvo, Andrea, Salamone, Paolina, Fuda, Giuseppe, Colosimo, Carlo, Spera, Cristina, Ranchicchio, Prabha Cristina, Stipa, Giuseppe, Frondizi, Domenico, Lunetta, Christian, Sansone, Valeria, Tarlarini, Claudia, Gerardi, Francesca, Silani, Vincenzo, Doretti, Alberto, Colombo, Eleonora, Demirtzidis, Gianluca, Tedeschi, Gioacchino, Trojsi, Francesca, Passaniti, Carla, Ballestrero, Stefania, Dorst, Johannes, Weiland, Ulrike, Fromm, Andrea, Wiesenfarth, Maximilian, Kandler, Katharina, Witzel, Simon, Otto, Markus, Schuster, Joachim, Meyer, Thomas, Maier, André, Kettemann, Dagmar, Petri, Susanne, Müschen, Lars, Wohnrade, Camilla, Sarikidi, Anastasia, Osmanovic, Alma, Grosskreutz, Julian, Rödiger, Annekathrin, Steinbach, Robert, Ilse, Benjamin, Smesny, Uta, Untucht, Robert, Günther, René, Vidovic, Maximilian, Shaw, Pamela, Collins, Alexis, Wollff, Helen, Walsh, Theresa, Tuddenham, Lee, Kazoka, Mbombe, White, David, Young, Stacy, Thompson, Benjamin, Madarshahian, Daniel, Chhetri, Suresh K, Chaouch, Amina, Young, Carolyn A, Arndt, Heike, Hanemann, Coliver, Lambert, Thomas, Beltran, Stephane, Couratier, Philippe, Esselin, Florence, Camu, William, De La Cruz, Elisa, Lemasson, Gwendal, Masrori, Pegah, Maguire, Sinead, Fogarty, Liz, Atoyebi, Toyosi, Obáin, Niamh Ní

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