Incorporation of Second-Tier Biomarker Testing Improves the Specificity of Newborn Screening for Mucopolysaccharidosis Type I von Peck, Dawn S, Lacey, Jean M, White, Amy L, Pino, Gisele, Studinski, April L, Fisher, Rachel, Ahmad, Ayesha, Spencer, Linda, Viall, Sarah, Shallow, Natalie, Siemon, Amy, Hamm, J Austin, Murray, Brianna K, Jones, Kelly L, Gavrilov, Dimitar, Oglesbee, Devin, Raymond, Kimiyo, Matern, Dietrich, Rinaldo, Piero, Tortorelli, Silvia

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Locoregional delivery of CAR-T cells in the clinic von Sagnella, Sharon M., White, Amy L., Yeo, Dannel, Saxena, Payal, van Zandwijk, Nico, Rasko, John E.J.

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Biochemical Diagnosis of Acute Hepatic Porphyria: Updated Expert Recommendations for Primary Care Physicians von Anderson, Karl E., Lobo, Raynah, Salazar, Denise, Schloetter, Mary, Spitzer, Gary, White, Amy L., Young, Randolph M., Bonkovsky, Herbert L., Frank, Elizabeth L., Mora, Jordanna, Tortorelli, Silvia

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The critical role of psychosine in screening, diagnosis, and monitoring of Krabbe disease von Guenzel, Adam J., Turgeon, Coleman T., Nickander, Kim K., White, Amy L., Peck, Dawn S., Pino, Gisele B., Studinski, April L., Prasad, Vinod K., Kurtzberg, Joanne, Escolar, Maria L., Lasio, Maria Laura Duque, Pellegrino, Joan E., Sakonju, Ai, Hickey, Rachel E., Shallow, Natalie M., Ream, Margie A., Orsini, Joseph J., Gelb, Michael H., Raymond, Kimiyo, Gavrilov, Dimitar K., Oglesbee, Devin, Rinaldo, Piero, Tortorelli, Silvia, Matern, Dietrich

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A new test method for biochemical analysis of plasmalogens in dried blood spots and erythrocytes from patients with peroxisomal disorders von Wegwerth, Peter J., White, Amy L., Stoway, Stephanie D., Loken, Perry R., Oglesbee, Devin, Matern, Dietrich, Tortorelli, Silvia, Raymond, Kimiyo M., Braverman, Nancy E., Gavrilov, Dimitar K.

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Natural history of rhizomelic chondrodysplasia punctata von White, Amy L., Modaff, Peggy, Holland-Morris, Francesca, Pauli, Richard M.

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Outcomes of newborn screening for Krabbe disease and their impact on selecting an effective screening approach von White, Amy L., Gavrilov, Dimitar, Pino, Gisele, Oglesbee, Devin, Peck, Dawn, Raymond, Kimiyo, Studinski, April, Tortorelli, Silvia, Matern, Dietrich

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Creating genetics-based infusion centers: a case study of two models von Laney, Dawn J., White, Amy L., Rhead, William J., Fernhoff, Paul

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Comparison of psychosine analysis in dried blood spots and red blood cells from children with Krabbe disease von White, Amy L., Escolar, Maria L., Peck, Dawn, Pino, Gisele, Studinski, April, Hoganson, George E., Kurtzberg, Joanne, Raymond, Kimiyo, Gavrilov, Dimitar, Oglesbee, Devin, Tortorelli, Silvia, Matern, Dietrich

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Laboratory follow up after abnormal newborn screening for lysosomal disorders von Peck, Dawn, Pino, Gessi Bentz, Studinksi, April, White, Amy L., Gavrilov, Dimitar, Oglesbee, Devin, Raymond, Kimiyo, Rinaldo, Piero, Tortorelli, Silvia, Matern, Dietrich

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Comparison of clinical practice guidelines and actual clinical practice in Fabry disease diagnosis von Laney, Dawn A., White, Amy L., Holida, Myrl, Clarke, Virginia, Lipinski, Shawn, Berry, Lisa, May, Katie, Long, Katie

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Incorporation of Second-Tier Biomarker Testing Improves the Specificity of Newborn Screening for Mucopolysaccharidosis Type I von Peck, Dawn S, Lacey, Jean M, White, Amy L, Pino, Gisele, Studinski, April L, Fisher, Rachel, Ahmad, Ayesha, Spencer, Linda, Viall, Sarah, Shallow, Natalie, Siemon, Amy, Hamm, J Austin, Murray, Brianna K, Jones, Kelly L, Gavrilov, Dimitar, Oglesbee, Devin, Raymond, Kimiyo, Matern, Dietrich, Rinaldo, Piero, Tortorelli, Silvia

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Panda bear inhaler von Berube, Patricia J, White, Amy L

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Panda bear inhaler von BERUBE PATRICIA J, WHITE AMY L

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Children's nasal spray containers and inhalers von BERUBE PATRICIA J, WHITE AMY L

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CHILDREN'S NASAL SPRAY CONTAINERS AND INHALERS von WHITE, AMY, L, RAYMOND, JENNIFER, BROOKS, BERUBE, PATRICIA, J

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CHILDREN'S NASAL SPRAY CONTAINERS AND INHALERS von WHITE, AMY, L, RAYMOND, JENNIFER, BROOKS, BERUBE, PATRICIA, J

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Children's nasal spray containers and inhalers von RAYMOND JENNIFER B, BERUBE PATRICIA J, WHITE AMY L

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Stool Microbiome and Metabolome Differences between Colorectal Cancer Patients and Healthy Adults von Weir, Tiffany L, Manter, Daniel K, Sheflin, Amy M, Barnett, Brittany A, Heuberger, Adam L, Ryan, Elizabeth P, White, Bryan A

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Exploring predictors of HIV-1 virologic failure to long-acting cabotegravir and rilpivirine: a multivariable analysis von Cutrell, Amy G., Schapiro, Jonathan M., Perno, Carlo F., Kuritzkes, Daniel R., Quercia, Romina, Patel, Parul, Polli, Joseph W., Dorey, David, Wang, Yongwei, Wu, Sterling, Van Eygen, Veerle, Crauwels, Herta, Ford, Susan L., Baker, Mark, Talarico, Christine L., Clair, Marty St, Jeffrey, Jerry, White, C. Thomas, Vanveggel, Simon, Vandermeulen, Kati, Margolis, David A., Aboud, Michael, Spreen, William R., van Lunzen, Jan

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