AAV-mediated delivery of zinc finger nucleases targeting hepatitis B virus inhibits active replication von Weber, Nicholas D, Stone, Daniel, Sedlak, Ruth Hall, De Silva Feelixge, Harshana S, Roychoudhury, Pavitra, Schiffer, Joshua T, Aubert, Martine, Jerome, Keith R

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Targeted DNA Mutagenesis for the Cure of Chronic Viral Infections von SCHIFFER, Joshua T, AUBERT, Martine, WEBER, Nicholas D, MINTZER, Esther, STONE, Daniel, JEROME, Keith R

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Gene therapy for progressive familial intrahepatic cholestasis type 3 in a clinically relevant mouse model von Weber, Nicholas D., Odriozola, Leticia, Martínez-García, Javier, Ferrer, Veronica, Douar, Anne, Bénichou, Bernard, González-Aseguinolaza, Gloria, Smerdou, Cristian

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CRISPR-Cas9 gene editing of hepatitis B virus in chronically infected humanized mice von Stone, Daniel, Long, Kelly R., Loprieno, Michelle A., De Silva Feelixge, Harshana S., Kenkel, Elizabeth J., Liley, R. Matt, Rapp, Stephen, Roychoudhury, Pavitra, Nguyen, Thuy, Stensland, Laurence, Colón-Thillet, Rossana, Klouser, Lindsay M., Weber, Nicholas D., Le, Connie, Wagoner, Jessica, Goecker, Erin A., Li, Alvason Zhenhua, Eichholz, Karsten, Corey, Lawrence, Tyrrell, D. Lorne, Greninger, Alexander L., Huang, Meei-Li, Polyak, Stephen J., Aubert, Martine, Sagartz, John E., Jerome, Keith R.

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Gene therapy for liver diseases — progress and challenges von Zabaleta, Nerea, Unzu, Carmen, Weber, Nicholas D., Gonzalez-Aseguinolaza, Gloria

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Rescue of infant progressive familial intrahepatic cholestasis type 3 mice by repeated dosing of AAV gene therapy von Weber, Nicholas D., Odriozola, Leticia, Ros-Gañán, Irene, García-Porrero, Guillermo, Salas, David, Argemi, Josepmaria, Combal, Jean-Philippe, Kishimoto, Takashi K., González-Aseguinolaza, Gloria

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A minimal bile salt excretory pump promoter allows bile acid-driven physiological regulation of transgene expression from a gene therapy vector von Martínez-García, Javier, Molina, Manuela, Odriozola, Leticia, Molina, Angie, González-Aseguinolaza, Gloria, Weber, Nicholas D, Smerdou, Cristian

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Gene Therapy for Acquired and Genetic Cholestasis von Martínez-García, Javier, Molina, Angie, González-Aseguinolaza, Gloria, Weber, Nicholas D., Smerdou, Cristian

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Novel vectors and approaches for gene therapy in liver diseases von Maestro, Sheila, Weber, Nicholas D., Zabaleta, Nerea, Aldabe, Rafael, Gonzalez-Aseguinolaza, Gloria

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mRNA and gene editing: Late breaking therapies in liver diseases von Zabaleta, Nerea, Torella, Laura, Weber, Nicholas D., Gonzalez‐Aseguinolaza, Gloria

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Digital detection of endonuclease mediated gene disruption in the HIV provirus von Sedlak, Ruth Hall, Liang, Shu, Niyonzima, Nixon, De Silva Feelixge, Harshana S., Roychoudhury, Pavitra, Greninger, Alexander L., Weber, Nicholas D., Boissel, Sandrine, Scharenberg, Andrew M., Cheng, Anqi, Magaret, Amalia, Bumgarner, Roger, Stone, Daniel, Jerome, Keith R.

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Comment on “Synthetic human ABCB4 mRNA therapy rescues severe liver disease phenotype in a BALB/c.Abcb4-/- mouse model of PFIC3” von Weber, Nicholas D., Martínez-García, Javier, González-Aseguinolaza, Gloria

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Use of an adeno‐associated virus serotype Anc80 to provide durable cure of phenylketonuria in a mouse model von Kaiser, Robert A., Weber, Nicholas D., Trigueros‐Motos, Laia, Allen, Kari L., Martinez, Michael, Cao, William, VanLith, Caitlin J., Hillin, Lori G., Douar, Anne, González‐Aseguinolaza, Gloria, Aldabe, Rafael, Lillegard, Joseph B.

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TALENs Targeting HBV: Designer Endonuclease Therapies for Viral Infections von Weber, Nicholas D, Stone, Daniel, Jerome, Keith R

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DNA cleavage enzymes for treatment of persistent viral infections: Recent advances and the pathway forward von Weber, Nicholas D, Aubert, Martine, Dang, Chung H, Stone, Daniel, Jerome, Keith R

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Novel vectors and approaches for gene therapy in liver diseasesKey points von Sheila Maestro, Nicholas D. Weber, Nerea Zabaleta, Rafael Aldabe, Gloria Gonzalez-Aseguinolaza

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Poster 194 Resolution of Thoracic Back Pain in Collegiate Runner after Ultrasound-Guided Costotransverse Joint Injection: A Case Report von Weber, Nicholas, DO, Helm, Eric R., MD

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AAV-Mediated Delivery of Zinc Finger Nucleases Targeting Hepatitis B Virus Inhibits Active Replication: e97579 von Weber, Nicholas D, Stone, Daniel, Sedlak, Ruth Hall, Feelixge, S DeSilva, Roychoudhury, Pavitra, Schiffer, Joshua T, Aubert, Martine, Jerome, Keith R

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Single Versus Two-Level Transforaminal Epidural Steroid Injection for Treating Lumbosacral Radicular Pain: What is the Evidence? von Cohen, Steven P., MD, Furman, Michael B., MD, MS, Weber, Nicholas H., DO, Singh, Jaspal Ricky, MD

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DELIVERING CRISPR THERAPEUTICS WITH LIPID NANOPARTICLES von WEBER, Nicholas D, LEE, Amy C. H

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