Safety and efficacy of tamoxifen in boys with Duchenne muscular dystrophy (TAMDMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial von Henzi, Bettina C, Schmidt, Simone, Nagy, Sara, Schaedelin, Sabine, Putananickal, Niveditha, Stimpson, Georgia, Ridout, Deborah, Muntoni, Francesco, Main, Marion, Abbott, Lianne, Burnett, Nicola, Rohwer, Anne-Marie, .O'Reilly, Emer, Guglieri, Michela, Bettolo, Chiara, James, Meredith, Sodhi, Jassi, Willis, Tracey, Rylance, Claire, Birchall, Nicola, Childs, Anne-Marie, Pysden, Karen, Martos-Lozano, Cristina, Pallant, Lindsey, Wadsworth, Steph, Gregson, Sarah, Clark, Stuart, Wraige, Elizabeth, Jungbluth, Heinz, Gowda, Vasantha, Sheehan, Ennie, Wolfe, Amy, Schofield, Alex, Hughes, Imelda, McCullagh, Gary, Whitehouse, Emily, Varma, Uma, Warner, Sinead, Reading, Emily, Benson, Lucy, Moustoukas, Jenny, Strachan, Kate, Emery, Nicholas, Ong, Min, Durso, Sarah, White, Kay, Hinde, Neil, Sanchez Marco, Silvia, Saxena, Anurag, Gibbon, Frances, Davis, Hayley, Murugan, Archana, Lynch, Mollie, Milton, Emily, Wills, Lucy, Robertson, Gemma, Cobb, Gavin, Burslem, Julie, Wong, Jarod, Brunklaus, Andreas, DiMarco, Marina, Brown, Sarah, Mckenzie, Susanne, Torne, Krupa, Mohamed, Rana, Velmurugan, Vel, Prasad, Manish, Williamson, Sarah, Degoede, Christian, Geary, Michelle, Palmer, Jenni, Shill, Catherine, White, Cathy, Gates, Sarah, Shah, Ayaz, .McFetridge, Jaci, Nic Fhirleinn, Grainne, Hussain, Nahin, Baskaran, Dhinesh, Lambat, Zubeida, Ambegaonkar, Gautam, Krishnakumar, Deepa, Taylor, Jacqui, Moores, Jo, Servais, Laurent, English, Hayley, Parasuraman, Deepak, Rabb, Rosanna, McMurchie, Heather, Deconinck, Nicolas, de Groot, Imelda, Horrocks, Iain, Houwen-van Opstal, Saskia, Laugel, Vincent, Lopez Lobato, Mercedes, Schara-Schmidt, Ulrike, von Moers, Arpad, Lawrence, Fiona, Hafner, Patricia, Dorchies, Olivier M

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Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy von Zambon, Alberto A., Ayyar Gupta, Vandana, Ridout, Deborah, Manzur, Adnan Y., Baranello, Giovanni, Trucco, Federica, Muntoni, Francesco, Tirupath, Sandya, Douglas, Melanie, McFetridge, Jaci, Parasuraman, Deepak, Alhaswani, Zoya, McMurchie, Heather, Rabb, Rosanna, Majumdar, Anirban, Vijayakumar, Kayal, Amin, Sam, Mason, Faye, Frimpong‐Ansah, Claire, Gibbon, Frances, Parson, Bethan, Naismith, Karen, Burslem, Julie, Baxter, Alex, Eadie, Clare, Horrocks, Iain, Di Marco, Marina, Childs, Anne‐Marie, Pallant, Lindsey, Spinty, Stefan, Shillington, Alison, Gregson, Sarah, Cheshman, Laura, Wraige, Elizabeth, Gowda, Vasantha, Jungbluth, Heinz, Sheehan, Jennie, Hughes, Imelda, Warner, Sinead, Straub, Volker, Guglieri, Michela, Mayhew, Anna, Chow, Gabby, Williamson, Sarah, Willis, Tracey, Kulshrestha, Richa, Emery, Nicholas, Ramdas, Sithara, Ramjattan, Hayley, de Goede, Christian, Selley, Andrea, Ong, Min, White, Kay, Illingworth, Marjorie, Geary, Michelle, Palmer, Jenni, White, Cathy, Greenfield, Kate, Hewawitharana, Gemunu, Julien, Yvonne, Stephens, Elma, Tewnion, Jane, Ambegaonkar, Gautam, Krishnakumar, Deepa, Taylor, Jacqui, Ward, Catherine, Willis, Tracey, Wright, Elizabeth, Rylance, Claire

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Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial von Mah, Jean K, Clemens, Paula R, Guglieri, Michela, Smith, Edward C, Finkel, Richard S, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Castro, Diana, Kuntz, Nancy L, McDonald, Craig M, Damsker, Jesse M, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Jackowski, Stefan, Stimpson, Georgia, Ridout, Deborah A, Ayyar-Gupta, Vandana, Baranello, Giovanni, Manzur, Adnan Y, Muntoni, Francesco, Gordish-Dressman, Heather, Leinonen, Mika, Ward, Leanne M, Hoffman, Eric P, Dang, Utkarsh J

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Functional outcome measures in young, steroid-naïve boys with Duchenne muscular dystrophy von Mayhew, Anna G, Moat, Dionne, McDermott, Michael P., Eagle, Michelle, Griggs, Robert C., King, Wendy M., James, Meredith K., Muni-Lofra, Robert, Shillington, Alison, Gregson, Sarah, Pallant, Lindsey, Skura, Christy, Staudt, Loretta A., Eichinger, Katy, McMurchie, Heather, Rabb, Rosanna, Di Marco, Marina, Brown, Sarah, Zanin, Riccardo, Arnoldi, Maria Teresa, McIntyre, Melissa, Wilson, Amelia, Alfano, Lindsay N., Lowes, Linda P., Blomgren, Colleen, Milev, Evelin, Iodice, Mario, Pasternak, Amy, Chiu, Angela, Lehnert, Ilka, Claus, Nicole, Dieruf, Kathy A., Rolle, Enrica, Nicorici, Alina, Andres, Barbara, Hobbiebrunken, Elke, Roetmann, Gerda, Kern, Victoria, Civitello, Matthew, Vogt, Sibylle, Hayes, Melissa J., Scholtes, Cheryl, Lacroix, Catherine, Gunn, Tara, Warner, Sinead, Newman, Jennifer, Barp, Andrea, Kundrat, Katherine, Kovelman, Staci, Powers, Penny J., Guglieri, Michela

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Efficacy and safety of onasemnogene abeparvovec in children with spinal muscular atrophy type 1: real-world evidence from 6 infusion centres in the United Kingdom von Gowda, Vasantha, Atherton, Mark, Murugan, Archana, Servais, Laurent, Sheehan, Jennie, Standing, Emma, Manzur, Adnan, Scoto, Mariacristina, Baranello, Giovanni, Munot, Pinki, McCullagh, Gary, Willis, Tracey, Tirupathi, Sandya, Horrocks, Iain, Dhawan, Anil, Eyre, Michael, Vanegas, Maria, Fernandez-Garcia, Miguel A., Wolfe, Amy, Pinches, Laura, Illingworth, Marjorie, Main, Marion, Abbott, Lianne, Smith, Hayley, Milton, Emily, D’Urso, Sarah, Vijayakumar, Kayal, Marco, Silvia Sanchez, Warner, Sinead, Reading, Emily, Douglas, Isobel, Muntoni, Francesco, Ong, Min, Majumdar, Anirban, Hughes, Imelda, Jungbluth, Heinz, Wraige, Elizabeth

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Epidemiology of Pediatric Critical Illness in a Population-Based Birth Cohort in Olmsted County, MN von Crow, Sheri S, Undavalli, Chaitanya, Warner, David O, Katusic, Slavica K, Kandel, Pujan, Murphy, Sinead L, Schroeder, Darrell R, Watson, R Scott

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Prebiotic‐supplemented partially hydrolysed cow's milk formula for the prevention of eczema in high‐risk infants: a randomized controlled trial von Boyle, R. J., Tang, M. L.‐K., Chiang, W. C., Chua, M. C., Ismail, I., Nauta, A., Hourihane, J. O'B., Smith, P., Gold, M., Ziegler, J., Peake, J., Quinn, P., Rao, R., Brown, N., Rijnierse, A., Garssen, J., Warner, J. O., Axelrad, Christine, Jeffries, Suzan, Donald, Yvette, Barham, Heather, Brown, Jenny, Wickenden, Rita, Barnes, Teresa, Taylor, Simone, Smith, Susan, Thomas, Natalie, Goh, Anne, Anng, Wong Anng, Hua, Christy Cao Yu, Daly, Deirdre, Lafford, Sinead, Cullinane, Claire, Bindels, Jacques, Merwe, Liandre, Klaassen, Dineke, Swinkels, Sophie, Knipping, Karen

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Assessing contractile ability of the quadriceps muscle using ultrasound imaging von Delaney, Sinead, Worsley, Peter, Warner, Martin, Taylor, Mark, Stokes, Maria

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Acyclovir and Transmission of HIV-1 from Persons Infected with HIV-1 and HSV-2 von Celum, C, Wald, A, Lingappa, J.R, Magaret, A.S, Wang, R.S, Mugo, N, Mujugira, A, Baeten, J.M, Mullins, J.I, Hughes, J.P, Bukusi, E.A, Cohen, C.R, Katabira, E, Ronald, A, Kiarie, J, Farquhar, C, Stewart, G.J, Makhema, J, Essex, M, Were, E, Fife, K.H, de Bruyn, G, Gray, G.E, McIntyre, J.A, Manongi, R, Kapiga, S, Coetzee, D, Allen, S, Inambao, M, Kayitenkore, K, Karita, E, Kanweka, W, Delany, S, Rees, H, Vwalika, B, Stevens, W, Campbell, M.S, Thomas, K.K, Coombs, R.W, Morrow, R, Whittington, W.L.H, McElrath, M.J, Barnes, L, Ridzon, R, Corey, L

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Preservation of swallowing in resected oral cavity squamous cell carcinoma: examining radiation volume effects (PRESERVE): study protocol for a randomized phase II trial von Lang, Pencilla, Contreras, Jessika, Kalman, Noah, Paterson, Claire, Bahig, Houda, Billfalk-Kelly, Astrid, Brennan, Sinead, Rock, Kathy, Read, Nancy, Venkatesan, Varagur, Sathya, Jinka, Mendez, Lucas C., MacNeil, S. Danielle, Nichols, Anthony C., Fung, Kevin, Mendez, Adrian, Winquist, Eric, Kuruvilla, Sara, Stewart, Paul, Warner, Andrew, Mitchell, Sylvia, Theurer, Julie A., Palma, David A.

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