Intravitreous injection of AAV2-sFLT01 in patients with advanced neovascular age-related macular degeneration: a phase 1, open-label trial von Heier, Jeffrey S, MD, Kherani, Saleema, MD, Desai, Shilpa, MD, Dugel, Pravin, MD, Kaushal, Shalesh, MD, Cheng, Seng H, PhD, Delacono, Cheryl, OD, Purvis, Annie, MSPH, Richards, Susan, PhD, Le-Halpere, Annaig, PharmD, Connelly, John, MBA, Wadsworth, Samuel C, PhD, Varona, Rafael, MD, Buggage, Ronald, MD, Scaria, Abraham, PhD, Campochiaro, Peter A, Prof

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Adeno-Associated Virus Gene Therapy for Liver Disease von Kattenhorn, Lisa M, Tipper, Christopher H, Stoica, Lorelei, Geraghty, Deborah S, Wright, Teresa L, Clark, K Reed, Wadsworth, Samuel C

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Aurintricarboxylic acid increases yield of HSV-1 vectors von Pechan, Peter, Ardinger, Jeffery, Ketavarapu, Jyothi, Rubin, Hillard, Wadsworth, Samuel C, Scaria, Abraham

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AAV5-mediated sFLT01 gene therapy arrests retinal lesions in Ccl2−/− /Cx3cr1−/− mice von Tuo, Jingsheng, Pang, Ji-Jing, Cao, Xiaoguang, Shen, Defen, Zhang, Jun, Scaria, Abraham, Wadsworth, Samuel C, Pechan, Peter, Boye, Sanford L, Hauswirth, William W, Chan, Chi-Chao

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AAVS1-Targeted Plasmid Integration in AAV Producer Cell Lines von Luo, Yuxia, Frederick, Amy, Martin, John M, Scaria, Abraham, Cheng, Seng H, Armentano, Donna, Wadsworth, Samuel C, Vincent, Karen A

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AAV2 Vector Harboring a Liver-Restricted Promoter Facilitates Sustained Expression of Therapeutic Levels of α-Galactosidase A and the Induction of Immune Tolerance in Fabry Mice von Ziegler, Robin J, Lonning, Scott M, Armentano, Donna, Li, Chester, Souza, David W, Cherry, Maribeth, Ford, Christine, Barbon, Christine M, Desnick, Robert J, Gao, Guangping, Wilson, James M, Peluso, Richard, Godwin, Simon, Carter, Barrie J, Gregory, Richard J, Wadsworth, Samuel C, Cheng, Seng H

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A Constitutively Active Hypoxia-Inducible Factor-1α/VP16 Hybrid Factor Activates Expression of the Human B-Type Natriuretic Peptide Gene von Luo, Yuxia, Jiang, Canwen, Belanger, Adam J., Akita, Geoffrey Y., Wadsworth, Samuel C., Gregory, Richard J., Vincent, Karen A.

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Aerosol and lobar administration of a recombinant adenovirus to individuals with cystic fibrosis. I. Methods, safety, and clinical implications von JOSEPH, Patricia M, O'SULLIVAN, Brian P, ST. GEORGE, Judith A, MEEKER, David P, LAPEY, Allen, DORKIN, Henry, OREN, Joseph, BALFOUR, Rosemary, PERRICONE, Michael A, ROSENBERG, Mireille, WADSWORTH, Samuel C, SMITH, Alan E

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Multiple forms of dynamin are encoded by shibire, a Drosophila gene involved in endocytosis von Chen, M.S, Obar, R.A, Schroeder, C.C, Austin, T.W, Poodry, C.A, Wadsworth, S.C, Vallee, R.B

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Aerosol and lobar administration of a recombinant adenovirus to individuals with cystic fibrosis. II. Transfection efficiency in airway epithelium von PERRICONE, Michael A, MORRIS, James E, SMITH, Alan E, WADSWORTH, Samuel C, ST. GEORGE, Judith A, PAVELKA, Karen, PLOG, Malinda S, O'SULLIVAN, Brian P, JOSEPH, Patricia M, DORKIN, Henry, LAPEY, Allen, BALFOUR, Rosemary, MEEKER, David P

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Scaleable chromatographic purification process for recombinant adeno-associated virus (rAAV) von O'Riordan, Catherine R., Lachapelle, Amy L., Vincent, Karen A., Wadsworth, Samuel C.

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Characterization of an adenovirus gene transfer vector containing an E4 deletion von Armentano, D, Sookdeo, C C, Hehir, K M, Gregory, R J, St George, J A, Prince, G A, Wadsworth, S C, Smith, A E

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460. Purification of AAV8 Using a Prototype Affinity Resin Compatible with cGMP Manufacturing von Dupuis, Colleen M., Medeiros, Amy A., Wadsworth, Samuel C., Clark, K. Reed, Morrison, Christopher J.

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710. Surface Adsorptive Loss of rAAV on Materials Used in cGMP Manufacturing von Jiang, Monica, Dupuis, Colleen M., Medeiros, Amy A., Wadsworth, Samuel C., Clark, K. Reed, Morrison, Christopher J.

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304. Particle Titer Determination and Characterization of rAAV Molecules Using Nanoparticle Tracking Analysis von Povlich, Samantha F., Mehtala, Jonathan G., Wilmes, Gwendolyn M., Morrison, Christopher J., Wadsworth, Samuel C., Clark, K. Reed

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E4ORF3 Requirement for Achieving Long-Term Transgene Expression from the Cytomegalovirus Promoter in Adenovirus Vectors von Armentano, D, Smith, M P, Sookdeo, C C, Zabner, J, Perricone, M A, St George, J A, Wadsworth, S C, Gregory, R J

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Adenovirus-Mediated Persistent Cystic Fibrosis Transmembrane Conductance Regulator Expression in Mouse Airway Epithelium von Scaria, A, St George, J A, Jiang, C, Kaplan, J M, Wadsworth, S C, Gregory, R J

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PEGylation of adenovirus with retention of infectivity and protection from neutralizing antibody in vitro and in vivo von O'RIORDAN, C. R, LACHAPELLE, A, DELGADO, C, PARKES, V, WADSWORTH, S. C, SMITH, A. E, FRANCIS, G. E

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670. Probing the Stability of rAAV Capsids and Genomic Constructs Using Differential Scanning Calorimetry in Concert With Mobile Phase Modifiers von Maratt, James D., Povlich, Samantha F., Morrison, Christopher J., Wilmes, Gwendolyn M., Wadsworth, Samuel C., Reed Clark, K.

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Adenoviral Vector Expressing ICP47 Inhibits Adenovirus-Specific Cytotoxic T Lymphocytes in Nonhuman Primates von Scaria, Abraham, Sullivan, Jennifer A., St. George, Judith A., Kaplan, Johanne M., Lukason, Michael J., Morris, James E., Plog, Malinda, Nicolette, Charles, Gregory, Richard J., Wadsworth, Samuel C.

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