DMD antisense oligonucleotide mediated exon skipping efficiency correlates with flanking intron retention time and target position within the exon von Goossens, Remko, Verwey, Nisha, Ariyurek, Yavuz, Schnell, Fred, Aartsma-Rus, Annemieke

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Non-sequential and multi-step splicing of the dystrophin transcript von Gazzoli, Isabella, Pulyakhina, Irina, Verwey, Nisha E., Ariyurek, Yavuz, Laros, Jeroen F. J., 't Hoen, Peter A. C., Aartsma-Rus, Annemieke

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Peripheral blood transcriptome profiling enables monitoring disease progression in dystrophic mice and patients von Signorelli, Mirko, Ebrahimpoor, Mitra, Veth, Olga, Hettne, Kristina, Verwey, Nisha, García‐Rodríguez, Raquel, Tanganyika‐deWinter, Christa L, Lopez Hernandez, Luz B, Escobar Cedillo, Rosa, Gómez Díaz, Benjamín, Magnusson, Olafur T, Mei, Hailiang, Tsonaka, Roula, Aartsma‐Rus, Annemieke, Spitali, Pietro

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Molecular signatures of age-associated chronic degeneration of shoulder muscles von Raz, Yotam, Henseler, Jan Ferdinand, Kolk, Arjen, Tatum, Zuotian, Groosjohan, Niels Kuipers, Verwey, Nisha E, Arindrarto, Wibowo, Kielbasa, Szymon M, Nagels, Jochem, 't Hoen, Peter A C, Nelissen, Rob G H H, Raz, Vered

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Antisense-Mediated Skipping of Dysferlin Exons in Control and Dysferlinopathy Patient-Derived Cells von Verwey, Nisha, Gazzoli, Isabella, Krause, Sabine, Mamchaoui, Kamel, Mouly, Vincent, Aartsma-Rus, Annemieke

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Longitudinal Assessment of Creatine Kinase, Creatine/Creatinineratio and Myostatin as Monitoring Biomarkers in Becker Muscular Dystrophy von van de Velde, Nienke M., Koeks, Zaïda, Signorelli, Mirko, Verwey, Nisha, Overzier, Maurice, Bakker, Jaap A., Sajeev, Gautam, Signorovitch, James, Ricotti, Valeria, Verschuuren, Jan, Brown, Kristy, Spitali, Pietro, Niks, Erik H.

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Antisense-Mediated Skipping of Dysferlin Exons in Control and Dysferlinopathy Patient-Derived Cells von Verwey, Nisha, Gazzoli, Isabella, Krause, Sabine, Mamchaoui, Kamel, Mouly, Vincent, Aartsma-Rus, Annemieke

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Longitudinal Assessment of Creatine Kinase, Creatine/Creatinine ratio , and Myostatin as Monitoring Biomarkers in Becker Muscular Dystrophy von van de Velde, Nienke M., Koeks, Zaïda, Signorelli, Mirko, Verwey, Nisha, Overzier, Maurice, Bakker, Jaap A., Sajeev, Gautam, Signorovitch, James, Ricotti, Valeria, Verschuuren, Jan, Brown, Kristy, Spitali, Pietro, Niks, Erik H.

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SplicePie: a novel analytical approach for the detection of alternative, non-sequential and recursive splicing von Pulyakhina, Irina, Gazzoli, Isabella, 't Hoen, Peter A C, Verwey, Nisha, den Dunnen, Johan T, den Dunnen, Johan, Aartsma-Rus, Annemieke, Laros, Jeroen F J

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A decline in PABPN1 induces progressive muscle weakness in oculopharyngeal muscle dystrophy and in muscle aging von Anvar, Seyed Yahya, Raz, Yotam, Verway, Nisha, van der Sluijs, Barbara, Venema, Andrea, Goeman, Jelle J, Vissing, John, van der Maarel, Silvère M, 't Hoen, Peter A C, van Engelen, Baziel G M, Raz, Vered

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SplicePie: a novel analytical approach for the detection of alternative, non-sequential and recursive splicing von Pulyakhina, Irina, Gazzoli, Isabella, 't Hoen, Peter A C, Verwey, Nisha, den Dunnen, Johan T, Aartsma-Rus, Annemieke, Laros, Jeroen F J

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A Novel Feed-Forward Loop between ARIH2 E3-Ligase and PABPN1 Regulates Aging-Associated Muscle Degeneration von Raz, Vered, Buijze, Hellen, Raz, Yotam, Verwey, Nisha, Anvar, Seyed Yahya, Aartsma-Rus, Annemieke, van der Maarel, Silvère M

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DMD antisense oligonucleotide mediated exon skipping efficiency correlates with flanking intron retention time and target position within the exon von Goossens, Remko, Verwey, Nisha, Ariyurek, Yavuz, Schnell, Fred, Aartsma-Rus, Annemieke

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DMD ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING EFFICIENCY von WU, Chia-Ling, GOOSSENS, Remko, AARTSMA-RUS, Annemieke, VERWEY, Nisha, ARIYUREK, Yavuz, SCHNELL, Frederick Joseph

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DMD ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING EFFICIENCY von WU, Chia-Ling, GOOSSENS, Remko, AARTSMA-RUS, Annemieke, VERWEY, Nisha, ARIYUREK, Yavuz, SCHNELL, Frederick Joseph

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