Intracerebral administration of rAAV2/5hNAGLU vector in children with MPS IIIB: results at 30 months of a phase I/II trial von Tardieu, Marc, Zerah, Michel, Gougeon, Marie-Lise, Ausseil, Jerome, de Bournonville, Stephanie, Husson, Beatrice, Zafeiriou, Dimitrios, Parenti, GianCarlo, Bourget, Philippe, Artaud, Cecile, Poirier, Beatrice, VanVlies, Noami, Deiva, Kumaran, Baugnon, Thomas, Roujeau, Thomas, Crystal, Ronald G, Richard, Charles, Heard, Jean-Michel

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