Safety and efficacy of zinpentraxin alfa as monotherapy or in combination with ruxolitinib in myelofibrosis: stage I of a phase II trial von Verstovsek, Srdan, Foltz, Lynda, Gupta, Vikas, Hasserjian, Robert, Manshouri, Taghi, Mascarenhas, John, Mesa, Ruben, Pozdnyakova, Olga, Ritchie, Ellen, Veletic, Ivo, Gamel, Katia, Hamidi, Habib, Han, Lyrialle, Higgins, Brian, Trunzer, Kerstin, Uguen, Marianne, Wang, Dao, El-Galaly, Tarec Christoffer, Todorov, Boyan, Gotlib, Jason

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Untreated bleeds in people with hemophilia A in a noninterventional study and intrapatient comparison after initiating emicizumab in HAVEN 1–3 von Callaghan, Michael U., Asikanius, Elina, Lehle, Michaela, Oldenburg, Johannes, Mahlangu, Johnny, Uguen, Marianne, Chebon, Sammy, Kruse‐Jarres, Rebecca, Jiménez‐Yuste, Víctor, Shima, Midori, Trask, Peter, Kempton, Christine L., Kessler, Craig M., Levy, Gallia G., Peyvandi, Flora

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Do pregnancies reduce iron overload in HFE hemochromatosis women? results from an observational prospective study von Scotet, Virginie, Saliou, Philippe, Uguen, Marianne, L'Hostis, Carine, Merour, Marie-Christine, Triponey, Céline, Chanu, Brigitte, Nousbaum, Jean-Baptiste, Le Gac, Gerald, Ferec, Claude

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A multicenter, open-label phase 3 study of emicizumab prophylaxis in children with hemophilia A with inhibitors von Young, Guy, Liesner, Ri, Chang, Tiffany, Sidonio, Robert, Oldenburg, Johannes, Jiménez-Yuste, Victor, Mahlangu, Johnny, Kruse-Jarres, Rebecca, Wang, Michael, Uguen, Marianne, Doral, Michelle Y., Wright, Lilyan Y., Schmitt, Christophe, Levy, Gallia G., Shima, Midori, Mancuso, Maria Elisa

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Phase 3 COMMODORE Trials of Crovalimab in Paroxysmal Nocturnal Hemoglobinuria (PNH): Impact on Kidney Function: SA-PO280 von Sreckovic, Sasha, Brocchieri, Cristian, Leon, Patty G., Balachandran, Nadiesh, Uguen, Marianne, Buatois, Simon

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Patient Preferences and Treatment Satisfaction in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Treated with Crovalimab and Approved C5 Inhibitors in the Phase III Random... von Kulasekararaj, Austin, Fernandez, Fernando Ataulfo Gonzalez, Scheinberg, Phillip, Straetmans, Nicole, Ueda, Yasutaka, Gentile, Brittany, Stefani, Jennifer, Uguen, Marianne, Roeth, Alexander

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Patient-Reported Outcomes (PROs) in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Treated with Crovalimab and Eculizumab: Results from the Phase III Randomized COMMODORE... von Panse, Jens, Cermak, Jaroslav, Kyselova, Olena, Gotoh, Akihiko, Sahin, Fahri, Schrezenmeier, Hubert, Chang, Alice C., Gentile, Brittany, Uguen, Marianne, Han, Bing

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WCN24-828 PHASE 3 COMMODORE TRIALS OF CROVALIMAB IN PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH): IMPACT ON KIDNEY FUNCTION von Soldati, Rocio, Sreckovic, Sasha, Brocchieri, Cristian, Leon, Patty, Balachandran, Nadiesh, Uguen, Marianne, Buatois, Simon

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Phase 3 randomized COMMODORE 1 trial: Crovalimab versus eculizumab in complement inhibitor‐experienced patients with paroxysmal nocturnal hemoglobinuria von Scheinberg, Phillip, Clé, Diego Villa, Kim, Jin Seok, Nur, Erfan, Yenerel, Mustafa N., Barcellini, Wilma, Bonito, Debora, Giai, Valentina, Hus, Marek, Lee, YooJin, Lekue, Cristina Barrenetxea, Panse, Jens, Ueda, Yasutaka, Buatois, Simon, Gentile, Brittany, Kiialainen, Anna, Patel, Himika, Sreckovic, Sasha, Uguen, Marianne, Edwards, John, Nagy, Zsolt, Kulasekararaj, Austin G.

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Health‐related quality of life and caregiver burden of emicizumab in children with haemophilia A and factor VIII inhibitors—Results from the HAVEN 2 study von Mancuso, Maria Elisa, Mahlangu, Johnny, Sidonio, Robert, Trask, Peter, Uguen, Marianne, Chang, Tiffany, Shima, Midori, Young, Guy, Oldenburg, Johannes, Mackensen, Sylvia

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Evaluation of Fatigue in Previously Untreated CLL Patients with Comorbidities Treated with Obinutuzumab (GA101) + Chlorambucil (GClb) or Rituximab + Chlorambucil (RClb) von Goede, Valentin, Trask, Peter C, Ziesel, Katharina, Uguen, Marianne, Bazeos, Alexandra, Fischer, Kirsten, Hallek, Michael

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HAVEN 2 Updated Analysis: Multicenter, Open-Label, Phase 3 Study to Evaluate Efficacy, Safety and Pharmacokinetics of Subcutaneous Administration of Emicizumab Prophylaxis in Pedia... von Young, Guy, Sidonio, Robert F., Liesner, Ri, Oldenburg, Johannes, Chang, Tiffany, Uguen, Marianne, Dhalluin, Christophe, Schmitt, Christophe, Levy, Gallia G., Shima, Midori, Mahlangu, Johnny

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Emicizumab Prophylaxis Provides Flexible and Effective Bleed Control in Children with Hemophilia Α with Inhibitors: Results from the HAVEN 2 Study von Young, Guy, Liesner, Ri, Sidonio, Robert F., Oldenburg, Johannes, Jimenez-Yuste, Victor, Mahlangu, Johnny, Kruse-Jarres, Rebecca, Wang, Michael, Chang, Tiffany, Uguen, Marianne, Doral, Michelle, Schmitt, Christophe, Levy, Gallia G., Shima, Midori, Mancuso, Maria Elisa

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Untreated Bleeds May Be Historically Under-Reported and More Prevalent in People with Hemophilia A with Inhibitors: An Examination of Bleed Data from a Prospective, Non-Interventio... von Callaghan, Michael U., Asikanius, Elina, Lehle, Michaela, Oldenburg, Johannes, Mahlangu, Johnny, Uguen, Marianne, Chebon, Sammy, Kruse-Jarres, Rebecca, Jimenez-Yuste, Victor, Shima, Midori, Trask, Peter, Kempton, Christine L., Kessler, Craig M., Levy, Gallia G., Santagostino, Elena

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Bleeding Events and Safety Outcomes in Patients with Hemophilia a with Inhibitors: A Prospective, Multicenter, Non-Interventional Study von Mahlangu, Johnny, Oldenburg, Johannes, Callaghan, Michael U, Shima, Midori, Santagostino, Elena, Lehle, Michaela, Uguen, Marianne, Hirst, Ceri, Moore, Maggie, Recht, Michael, Garcia, Claudia, Yang, Renchi, Kruse-Jarres, Rebecca

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Updated Survival Analysis from the CLL11 Study: Obinutuzumab Versus Rituximab in Chemoimmunotherapy-Treated Patients with Chronic Lymphocytic Leukemia von Goede, Valentin, Fischer, Kirsten, Bosch, Francesc, Follows, George, Frederiksen, Henrik, Cuneo, Antonio, Ludwig, Heinz, Crompton, Noelle, Maurer, Joerg, Uguen, Marianne, Fingerle-Rowson, Gunter, Hallek, Michael

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THU-466 Treatment with Atezolizumab-Bevacizumab for hepatocellular carcinoma in the french population outside clinical trials: data from the prospective CHIEF cohort von Allaire, Manon, Hajer, Ben Khadhra, Amaddeo, Giuliana, Bouattour, Mohamed, Brusset, Bleuenn, Ziol, Marianne, Merle, Philippe, Blanc, Jean-Frédéric, Uguen, Thomas, Ganne-Carrié, Nathalie, Cattan, Stéphane, Riachi, Ghassan, Loustaud-Ratti, Veronique, Decaens, Thomas, Silvain, Christine, Peron, Jean Marie, Baron, Aurore, Pageaux, Georges-Philippe, Oberti, Frédéric, Anty, Rodolphe, Manfredi, Sylvain, Bourliere, Marc, Ben Merabet, Yasmina, Nousbaum, JeanB-aptiste, Heurgue-Berlot, Alexandra, Ollivier-Hourmand, Isabelle, Ducournau, Gerard, Ganry, Olivier, Costentin, Charlotte, Khac, Eric Nguyen

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Nestin as a diagnostic and prognostic marker for combined hepatocellular-cholangiocarcinoma von Calderaro, Julien, Di Tommaso, Luca, Maillé, Pascale, Beaufrère, Aurélie, Nguyen, Cong Trung, Heij, Lara, Gnemmi, Viviane, Graham, Rondell P., Charlotte, Frédéric, Chartier, Suzanne, Wendum, Dominique, Vij, Mukul, Allende, Daniela, Diaz, Alba, Fuster, Carla, Rivière, Benjamin, Herrero, Astrid, Augustin, Jérémy, Evert, Katja, Calvisi, Diego Francesco, Leow, Wei Qiang, Leung, Howard Ho Wai, Bednarsch, Jan, Boleslawski, Emmanuel, Rela, Mohamed, Chan, Anthony Wing-Hung, Forner, Alejandro, Reig, Maria, Pujals, Anaïs, Favre, Loetitia, Allaire, Manon, Scatton, Olivier, Uguen, Arnaud, Trépo, Eric, Sanchez, Lukas Otero, Chatelain, Denis, Remmelink, Myriam, Boulagnon-Rombi, Camille, Bazille, Céline, Sturm, Nathalie, Menahem, Benjamin, Frouin, Eric, Tougeron, David, Tournigand, Christophe, Kempf, Emmanuelle, Kim, Haeryoung, Ningarhari, Massih, Michalak-Provost, Sophie, Kather, Jakob Nikolas, Gouw, Annette S.H., Gopal, Purva, Brustia, Raffaele, Vibert, Eric, Schulze, Kornelius, Rüther, Darius F., Weidemann, Sören A., Rhaiem, Rami, Nault, Jean-Charles, Laurent, Alexis, Amaddeo, Giuliana, Regnault, Hélène, de Martin, Eleonora, Sempoux, Christine, Navale, Pooja, Shinde, Jayendra, Bacchuwar, Ketan, Westerhoff, Maria, Lo, Regina Cheuk-Lam, Sebbagh, Mylène, Guettier, Catherine, Lequoy, Marie, Komuta, Mina, Ziol, Marianne, Paradis, Valérie, Shen, Jeanne, Caruso, Stefano

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Familial transmission of chromoanagenesis leads to unpredictable unbalanced rearrangements through meiotic recombination von Masson, Julie, Pebrel-Richard, Céline, Egloff, Matthieu, Frétigny, Mathilde, Beaumont, Marion, Uguen, Kevin, Rollat-Farnier, Pierre‐antoine, Diguet, Flavie, Perthus, Isabelle, Le Gudayer, Gwenaël, Haye, Damien, Dupeyron, Marie‐noëlle Bonnet, Putoux, Audrey, Raskin-Champion, Fabienne, Till, Marianne, Chatron, Nicolas, Doray, Bérénice, Bardel, Claire, Vinciguerra, Christine, Sanlaville, Damien, Schluth-Bolard, Caroline

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Familial transmission of chromoanagenesis leads to unpredictable unbalanced rearrangements through meiotic recombination von Masson, Julie, Pebrel‐Richard, Céline, Egloff, Matthieu, Frétigny, Mathilde, Beaumont, Marion, Uguen, Kevin, Rollat‐Farnier, Pierre‐Antoine, Diguet, Flavie, Perthus, Isabelle, Le Gudayer, Gwenaël, Haye, Damien, Dupeyron, Marie‐Noëlle Bonnet, Putoux, Audrey, Raskin‐Champion, Fabienne, Till, Marianne, Chatron, Nicolas, Doray, Bérénice, Bardel, Claire, Vinciguerra, Christine, Sanlaville, Damien, Schluth‐Bolard, Caroline

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