Predictors of Loss of Ambulation in Duchenne Muscular Dystrophy: A Systematic Review and Meta-Analysis von Landfeldt, E., Alemán, A., Abner, S., Zhang, R., Werner, C., Tomazos, I., Ferizovic, N., Lochmüller, H., Kirschner, J.

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Factors Associated with Respiratory Health and Function in Duchenne Muscular Dystrophy: A Systematic Review and Evidence Grading von Landfeldt, E., Aleman, A., Abner, S., Zhang, R., Werner, C., Tomazos, I., Lochmüller, H., Quinlivan, R.M.

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Low Rate of Clinically Evident Extravascular Hemolysis in Patients with Paroxysmal Nocturnal Hemoglobinuria Treated with a Complement C5 Inhibitor: Results from a Large, Multicente... von Shammo, Jamile, Gajra, Ajeet, Patel, Yogesh, Tomazos, Ioannis, Kish, Jonathan, Hill, Anita, Sierra, J. Rafael, Araten, David

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Long-term participation 7-8 years after stroke: Experiences of people in working-age von Törnbom, Karin, Lundälv, Jörgen, Sunnerhagen, Katharina S

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Body fat distribution and risk of incident ischemic stroke in men and women aged 50 to 74 years from the general population. The KORA Augsburg cohort study von Zahn, Karl, Linseisen, Jakob, Heier, Margit, Peters, Annette, Thorand, Barbara, Nairz, Franziska, Meisinger, Christa

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Low body mass index negatively affects muscle mass and intramuscular fat of chronic stroke survivors von Akazawa, Naoki, Harada, Kazuhiro, Okawa, Naomi, Tamura, Kimiyuki, Moriyama, Hideki

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PB1934: REAL‐WORLD OUTCOMES OF ECULIZUMAB TREATMENT IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINUREA: A SYSTEMATIC LITERATURE REVIEW AND EVIDENCE SYNTHESIS von Nishimura, J.‐I., Popoff, E., Cheung, A., Wang, A., Tomazos, I., Szer, J.

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P813: EFFICACY, TREATMENT ADMINISTRATION SATISFACTION AND SAFETY OF SUBCUTANEOUS RAVULIZUMAB THROUGH 1 YEAR IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA WHO RECEIVED PRIOR... von Yenerel, M. N., Sicre de Fontbrune, F., Piatek, C., Sahin, F., Füreder, W., Ogawa, M., Tomazos, I., Doll, H., Ozol-Godfrey, A., Sierra, J. R., Szer, J.

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Towards precision critical care management of blood pressure in hemorrhagic stroke patients using dynamic linear models von Liu, Yuzhe, Manners, Jody, Bittar, Yazan, Chou, Sherry H-Y, Gopalakrishnan, Vanathi

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Risk of ischemic stroke after discharge from inpatient surgery: Does the type of surgery matter? von Hsieh, Cheng-Yang, Huang, Chin-Wei, Wu, Darren Philbert, Sung, Sheng-Feng

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PRO77 Preliminary Characterization of Eculizumab Treatment Patterns, Preceding Disease Triggers and Supportive Therapies in Atypical Hemolytic Uremic Syndrome: A US Claims Database... von Tomazos, I., Levy, A., Faria, C.

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PRO33 Ravulizumab Reduces Productivity Losses Versus Eculizumab for Treating Atypical Hemolytic Uremic Syndrome: A 'cost Consequence' Analysis in 4 Countries von Levy, A., Chen, P., Tomazos, I.

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PRO5 COMPARING PRODUCTIVITY LOSSES FROM TREATING ATYPICAL HEMOLYTIC UREMIC SYNDROME PATIENTS IN THE UNITED STATES WITH ECULIZUMAB OR RAVULIZUMAB IN AN INFUSION CLINIC OR AT HOME von Levy, A., Chen, P.G.F., Tomazos, I.

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CO202 Relationship between Loss of Ambulation (LoA) and Timing of Pulmonary Outcomes Among Boys with Duchenne Muscular Dystrophy (DMD) von Gordish-Dressman, H.., Zhang, R., Kamstra, R., Werner, C., Morrison, K., Tomazos, I.

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CO120 Progression of Disease Burden Among Boys with Duchenne Muscular Dystrophy (DMD) According to Ambulatory Status and Age at Loss of Ambulation (LoA) von Gordish-Dressman, H.., Zhang, R., Kamstra, R., Werner, C., Liu, E., Morrison, K., Tomazos, I.

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CO160 Relationship between Loss of Ambulation (LoA), Disease Burden, and Physical Functioning Among Boys with Duchenne Muscular Dystrophy (DMD) von Gordish-Dressman, H.., Zhang, R., Kamstra, R., Werner, C., Liu, E., Morrison, K., Tomazos, I.

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PCR238 Estimating Health State Utilities (HSUS) for Aromatic L-Amino Acid Decarboxylase Deficiency (AADCD) in the United States von Monteleone, B, Zhang, R, Forster, K, Chua, GN, Lloyd, A, Castellano, P, Tomazos, I

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CO105 A Retrospective Study Characterizing Age at Loss of Ambulation Among Patients With Friedreich Ataxia Using Health Administrative Claims Data in the United States von Salvucci, A., Qian, C., Powell, L., Lynch, D., Vasco, G., Johnston, K., Tomazos, I.

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CO142 A Retrospective Study Characterizing Age at Key Clinical Disease Indicators Among Patients With Friedreich Ataxia Using Health Administrative Claims Data in the United States von Salvucci, A., Qian, C., Powell, L., Lynch, D., Vasco, G., Johnston, K., Tomazos, I.

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PCR139 'We Have Conversations That Other Couples Don′t Have to Have:' A Qualitative Study of the Impact of Caregiving in Friedreich Ataxia (FA) von Szabo, S., Bever, A., Lynch, D., Vasco, G., Giunti, P., Vallortigara, J., Tomazos, I.

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