Reduced Intensity Conditioned Bone Marrow Transplant with Post-Transplant Cyclophosphamide and Donor-Derived Mesenchymal Stromal Cell Infusions for Recessive Dystrophic Epidermolys... von Ebens, Christen L., McGrath, John A, Tamai, Katsuto, Alain, Hovnanian, Wagner, John E., Riddle, Megan, Keene, Douglas R, DeFor, Todd E., Tryon, Rebecca, Chen, Mei, Woodley, David T, Hook, Kristin, Tolar, Jakub L

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Audacity of gene therapy von Dimitrov, Marketa, Ebens, Christen L, Tolar, Jakub

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Rapid Induction of Cerebral Organoids From Human Induced Pluripotent Stem Cells Using a Chemically Defined Hydrogel and Defined Cell Culture Medium von Lindborg, Beth A., Brekke, John H., Vegoe, Amanda L., Ulrich, Connor B., Haider, Kerri T., Subramaniam, Sandhya, Venhuizen, Scott L., Eide, Cindy R., Orchard, Paul J., Chen, Weili, Wang, Qi, Pelaez, Francisco, Scott, Carolyn M., Kokkoli, Efrosini, Keirstead, Susan A., Dutton, James R., Tolar, Jakub, O'Brien, Timothy D.

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Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases von Osborn, Mark J, Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, Tennis, Nicole, DeFeo, Anthony P, McElroy, Amber N, Starker, Colby G, Lee, Catherine, Merkel, Sarah, Lund, Troy C, Kelly-Spratt, Karen S, Jensen, Michael C, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Gabriel, Richard, Hippen, Keli L, Miller, Jeffrey S, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R

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Evolution of an adenine base editor into a small, efficient cytosine base editor with low off-target activity von Neugebauer, Monica E., Hsu, Alvin, Arbab, Mandana, Krasnow, Nicholas A., McElroy, Amber N., Pandey, Smriti, Doman, Jordan L., Huang, Tony P., Raguram, Aditya, Banskota, Samagya, Newby, Gregory A., Tolar, Jakub, Osborn, Mark J., Liu, David R.

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latent human herpesvirus-6A genome specifically integrates in telomeres of human chromosomes in vivo and in vitro von Arbuckle, Jesse H, Medveczky, Maria M, Luka, Janos, Hadley, Stephen H, Luegmayr, Andrea, Ablashi, Dharam, Lund, Troy C, Tolar, Jakub, De Meirleir, Kenny, Montoya, Jose G, Komaroff, Anthony L, Ambros, Peter F, Medveczky, Peter G

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Beyond the Surface: A Narrative Review Examining the Systemic Impacts of Recessive Dystrophic Epidermolysis Bullosa von Popp, Courtney, Miller, William, Eide, Cindy, Tolar, Jakub, McGrath, John A., Ebens, Christen L.

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Phage-assisted evolution and protein engineering yield compact, efficient prime editors von Doman, Jordan L., Pandey, Smriti, Neugebauer, Monica E., An, Meirui, Davis, Jessie R., Randolph, Peyton B., McElroy, Amber, Gao, Xin D., Raguram, Aditya, Richter, Michelle F., Everette, Kelcee A., Banskota, Samagya, Tian, Kathryn, Tao, Y. Allen, Tolar, Jakub, Osborn, Mark J., Liu, David R.

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Reliability and validity of the instrument for scoring clinical outcomes of research for epidermolysis bullosa (iscorEB) von Bruckner, A.L., Fairclough, D.L., Feinstein, J.A., Lara‐Corrales, I., Lucky, A.W., Tolar, J., Pope, E.

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Retinoblastoma tumor cell proliferation is negatively associated with an immune gene expression signature and increased immune cells von Sarver, Aaron L., Xie, Chencheng, Riddle, Megan J., Forster, Colleen L., Wang, Xiaohong, Lu, Huarui, Wagner, Wyatt, Tolar, Jakub, Hallstrom, Timothy C.

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Radiation Sparing Reduced Intensity Conditioning for Allogeneic Cell Transplantation in Patients with Dyskeratosis Congenita Comparable to Standard of Care: A Phase III Single Inst... von Dimitrov, Marketa, Merkle, Svatava, Vercellotti, Gregory M., Holtan, Shernan G, Tolar, Jakub, Ebens, Christen L.

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MECHANISMS OF DISEASE: Osteopetrosis von Tolar, Jakub, Teitelbaum, Steven L, Orchard, Paul J

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Interrogation of RDEB epidermal allografts after BMT reveals co-expression of collagen VII and keratin 15 with proinflammatory immune cells and fibroblasts von Riedl, Julia A., Riddle, Megan, Xia, Lily, Eide, Cindy, Boull, Christina, Ebens, Christen L., Tolar, Jakub

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Toxic Epidermal Necrolysis in Recessive Dystrophic Epidermolysis Bullosa following Bone Marrow Transplantation von Boull, Christina L., MD, Hylwa, Sara A., MD, Sajic, Dusan, MD, Wagner, John E., MD, Tolar, Jakub, MD, PhD, Hook, Kristen P., MD

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Methods for Decreasing Preweaning Mortality in a Fragile Mouse Model of Hypomorphic Collagen VII Deficiency von Strege, Chloe L, Miller, William C, Eide, Cindy, Hubbard, Jennifer, Tolar, Jakub

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Retention of epigenetic and transcriptional memory among reprogrammed T cells (T-iPSCs) imparts selective advantage for T cell re-differentiation von Williams, Robin L, Morrow, Alyssa, Allred, Jeremy, Tolar, Jakub, Haining, W. Nicholas, Yosef, Nir, Blazar, Bruce R

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Bone marrow myeloid-derived suppressor cells (MDSCs) inhibit graft-versus-host disease (GVHD) via an arginase-1–dependent mechanism that is up-regulated by interleukin-13 von Highfill, Steven L., Rodriguez, Paulo C., Zhou, Qing, Goetz, Christine A., Koehn, Brent H., Veenstra, Rachelle, Taylor, Patricia A., Panoskaltsis-Mortari, Angela, Serody, Jonathan S., Munn, David H., Tolar, Jakub, Ochoa, Augusto C., Blazar, Bruce R.

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Potential of Systemic Allogeneic Mesenchymal Stromal Cell Therapy for Children with Recessive Dystrophic Epidermolysis Bullosa von Petrof, Gabriela, Lwin, Su M., Martinez-Queipo, Magdalena, Abdul-Wahab, Alya, Tso, Simon, Mellerio, Jemima E., Slaper-Cortenbach, Ineke, Boelens, Jaap J., Tolar, Jakub, Veys, Paul, Ofuya, Mercy, Peacock, Janet L., Martinez, Anna E., McGrath, John A.

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Interrogation of RDEB Epidermal Allografts after BMT Reveals Coexpression of Collagen VII and Keratin 15 with Proinflammatory Immune Cells and Fibroblasts von Riedl, Julia A., Riddle, Megan, Xia, Lily, Eide, Cindy, Boull, Christina, Ebens, Christen L., Tolar, Jakub

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Methods for Decreasing Preweaning Mortality in a Fragile Mouse Model of Hypomorphic Collagen VII Deficiency von Strege, Chloe L, Miller, William C, Eide, Cindy, Hubbard, Jennifer, Tolar, Jakub

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