A Muscleblind Knockout Model for Myotonic Dystrophy von Kanadia, Rahul N., Johnstone, Karen A., Mankodi, Ami, Lungu, Codrin, Thornton, Charles A., Esson, Douglas, Timmers, Adrian M., Hauswirth, William W., Swanson, Maurice S.

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Restoration of cone vision in a mouse model of achromatopsia von Alexander, John J, Umino, Yumiko, Everhart, Drew, Chang, Bo, Min, Seok H, Li, Qiuhong, Timmers, Adrian M, Hawes, Norman L, Pang, Ji-jing, Barlow, Robert B, Hauswirth, William W

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Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis von Min, Seok H, Molday, Laurie L, Seeliger, Mathias W, Dinculescu, Astra, Timmers, Adrian M, Janssen, Andreas, Tonagel, Felix, Tanimoto, Naoyuki, Weber, Bernhard H F, Molday, Robert S, Hauswirth, William W

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Ocular Inflammatory Response to Intravitreal Injection of Adeno-Associated Virus Vector: Relative Contribution of Genome and Capsid von Timmers, Adrian M, Newmark, Judith A, Turunen, Heikki T, Farivar, Tanaz, Liu, Jilin, Song, Chunjuan, Ye, Guo-Jie, Pennock, Steven, Gaskin, Chantelle, Knop, David R, Shearman, Mark S

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Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy von Song, Chunjuan, Dufour, Valérie L, Cideciyan, Artur V, Ye, Guo-Jie, Swider, Malgorzata, Newmark, Judith A, Timmers, Adrian M, Robinson, Paulette M, Knop, David R, Chulay, Jeffrey D, Jacobson, Samuel G, Aguirre, Gustavo D, Beltran, William A, Shearman, Mark S

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Anti-apoptotic effects of CNTF gene transfer on photoreceptor degeneration in experimental antibody-induced retinopathy von ADAMUS, Grazyna, SUGDEN, Brad, SHIRAGA, Sharon, TIMMERS, Adrian M, HAUSWIRTH, William W

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Cone-specific expression using a human red opsin promoter in recombinant AAV von Li, Qiuhong, Timmers, Adrian M., Guy, John, Pang, Jijing, Hauswirth, William W.

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Preventing Stem Cell Incorporation into Choroidal Neovascularization by Targeting Homing and Attachment Factors von Sengupta, Nilanjana, Caballero, Sergio, Mames, Robert N, Timmers, Adrian M, Saban, Daniel, Grant, Maria B

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Human Blue-Opsin Promoter Preferentially Targets Reporter Gene Expression to Rat S-Cone Photoreceptors von Glushakova, Lyudmyla G, Timmers, Adrian M, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W

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AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice von Hennig, Anne K, Ogilvie, Judith Mosinger, Ohlemiller, Kevin K, Timmers, Adrian M, Hauswirth, William W, Sands, Mark S

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Ribozyme knockdown of the γ-subunit of rod cGMP phosphodiesterase alters the ERG and retinal morphology in wild-type mice von JIANWEN LIU, TIMMERS, Adrian M, LEWIN, Alfred S, HAUSWIRTH, William W

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Does recombinant adeno-associated virus-vectored proximal region of mouse rhodopsin promoter support only rod-type specific expression in vivo? von Glushakova, Lyudmyla G, Timmers, Adrian M, Issa, Tawfik M, Cortez, Nenita G, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W

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Characterization of intraocular immunopathology following intracameral inoculation with alloantigen von Saban, Daniel R, Elder, Ian A, Nguyen, Cuong Q, Smith, W Clay, Timmers, Adrian M, Grant, Maria B, Peck, Ammon B

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Decreased Expression of the Insulin-like Growth Factor 1 Receptor by Ribozyme Cleavage von Shaw, Lynn C, Afzal, Aqeela, Lewin, Alfred S, Timmers, Adrian M, Spoerri, Polyxenie E, Grant, Maria B

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Inactivation of the Basigin gene impairs normal retinal development and maturation von Ochrietor, Judith D, Moroz, Tatiana P, Clamp, Michael F, Timmers, Adrian M, Muramatsu, Takashi, Linser, Paul J

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Noninvasive Imaging by Optical Coherence Tomography to Monitor Retinal Degeneration in the Mouse von Li, Qiuhong, Timmers, Adrian M, Hunter, Kirk, Gonzalez-Pola, Carlos, Lewin, Alfred S, Reitze, David H, Hauswirth, William W

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Subretinal injections in rodent eyes: effects on electrophysiology and histology of rat retina von Timmers, A M, Zhang, H, Squitieri, A, Gonzalez-Pola, C

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Cone-specific expression using a human red opsin promoter in recombinant AAV: Retinal Degeneration and Gene Therapy von QIUHONG LI, TIMMERS, Adrian M, GUY, John, JIJING PANG, HAUSWIRTH, William W

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Ribozyme-targeted destruction of RNA associated with autosomal-dominant retinitis pigmentosa von DRENSER, K. A, TIMMERS, A. M, HAUSWIRTH, W. W, LEUWIN, A. S

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ADENO-ASSOCIATED VIRUS (AAV) SYSTEMS FOR TREATMENT OF PROGRANULIN ASSOCIATED NEURODEGENERATIVE DISEASES OR DISORDERS von Mandapati, Savitri, Shearman, Mark, Newmark, Judith, Pennock, Steven, Timmers, Adrian M, Li, Juan, Farivar, Tanaz

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