Ocular Inflammatory Response to Intravitreal Injection of Adeno-Associated Virus Vector: Relative Contribution of Genome and Capsid von Timmers, Adrian M, Newmark, Judith A, Turunen, Heikki T, Farivar, Tanaz, Liu, Jilin, Song, Chunjuan, Ye, Guo-Jie, Pennock, Steven, Gaskin, Chantelle, Knop, David R, Shearman, Mark S

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A Muscleblind Knockout Model for Myotonic Dystrophy von Kanadia, Rahul N., Johnstone, Karen A., Mankodi, Ami, Lungu, Codrin, Thornton, Charles A., Esson, Douglas, Timmers, Adrian M., Hauswirth, William W., Swanson, Maurice S.

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Restoration of cone vision in a mouse model of achromatopsia von Alexander, John J, Umino, Yumiko, Everhart, Drew, Chang, Bo, Min, Seok H, Li, Qiuhong, Timmers, Adrian M, Hawes, Norman L, Pang, Ji-jing, Barlow, Robert B, Hauswirth, William W

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Dose Range Finding Studies with Two RPGR Transgenes in a Canine Model of X-Linked Retinitis Pigmentosa Treated with Subretinal Gene Therapy von Song, Chunjuan, Dufour, Valérie L, Cideciyan, Artur V, Ye, Guo-Jie, Swider, Malgorzata, Newmark, Judith A, Timmers, Adrian M, Robinson, Paulette M, Knop, David R, Chulay, Jeffrey D, Jacobson, Samuel G, Aguirre, Gustavo D, Beltran, William A, Shearman, Mark S

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Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis von Min, Seok H, Molday, Laurie L, Seeliger, Mathias W, Dinculescu, Astra, Timmers, Adrian M, Janssen, Andreas, Tonagel, Felix, Tanimoto, Naoyuki, Weber, Bernhard H F, Molday, Robert S, Hauswirth, William W

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Cone-specific expression using a human red opsin promoter in recombinant AAV von Li, Qiuhong, Timmers, Adrian M., Guy, John, Pang, Jijing, Hauswirth, William W.

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Preventing Stem Cell Incorporation into Choroidal Neovascularization by Targeting Homing and Attachment Factors von Sengupta, Nilanjana, Caballero, Sergio, Mames, Robert N, Timmers, Adrian M, Saban, Daniel, Grant, Maria B

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Human Blue-Opsin Promoter Preferentially Targets Reporter Gene Expression to Rat S-Cone Photoreceptors von Glushakova, Lyudmyla G, Timmers, Adrian M, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W

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Anti-apoptotic effects of CNTF gene transfer on photoreceptor degeneration in experimental antibody-induced retinopathy von ADAMUS, Grazyna, SUGDEN, Brad, SHIRAGA, Sharon, TIMMERS, Adrian M, HAUSWIRTH, William W

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AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice von Hennig, Anne K, Ogilvie, Judith Mosinger, Ohlemiller, Kevin K, Timmers, Adrian M, Hauswirth, William W, Sands, Mark S

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Structural and Functional Protection of Photoreceptors from MNU-Induced Retinal Degeneration by the X-Linked Inhibitor of Apoptosis von Petrin, Dino, Baker, Adam, Coupland, Stuart G, Liston, Peter, Narang, Monica, Damji, Karim, Leonard, Brian, Chiodo, Vince A, Timmers, Adrian, Hauswirth, William, Korneluk, Robert G, Tsilfidis, Catherine

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AAV Gene Augmentation of Truncated Complement Factor H Differentially Rescues Ocular Complement Dysregulation in a Mouse Model von Grigsby, Daniel, Klingeborn, Mikael, Kelly, Una, Chew, Lindsey A, Asokan, Aravind, Devlin, Garth, Smith, Sharon, Keyes, Lisa, Timmers, Adrian, Scaria, Abraham, Bowes Rickman, Catherine

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Ribozyme knockdown of the γ-subunit of rod cGMP phosphodiesterase alters the ERG and retinal morphology in wild-type mice von JIANWEN LIU, TIMMERS, Adrian M, LEWIN, Alfred S, HAUSWIRTH, William W

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Does recombinant adeno-associated virus-vectored proximal region of mouse rhodopsin promoter support only rod-type specific expression in vivo? von Glushakova, Lyudmyla G, Timmers, Adrian M, Issa, Tawfik M, Cortez, Nenita G, Pang, Jijing, Teusner, Jacqueline T, Hauswirth, William W

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Characterization of intraocular immunopathology following intracameral inoculation with alloantigen von Saban, Daniel R, Elder, Ian A, Nguyen, Cuong Q, Smith, W Clay, Timmers, Adrian M, Grant, Maria B, Peck, Ammon B

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Toxicity and Efficacy Evaluation of an Adeno-Associated Virus Vector Expressing Codon-Optimized RPGR Delivered by Subretinal Injection in a Canine Model of X-linked Retinitis Pigme... von Dufour, Valérie L, Cideciyan, Artur V, Ye, Guo-Jie, Song, Chunjuan, Timmers, Adrian, Habecker, Perry L, Pan, Wei, Weinstein, Nicole M, Swider, Malgorzata, Durham, Amy C, Ying, Gui-Shuang, Robinson, Paulette M, Jacobson, Samuel G, Knop, David R, Chulay, Jeffrey D, Shearman, Mark S, Aguirre, Gustavo D, Beltran, William A

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Decreased Expression of the Insulin-like Growth Factor 1 Receptor by Ribozyme Cleavage von Shaw, Lynn C, Afzal, Aqeela, Lewin, Alfred S, Timmers, Adrian M, Spoerri, Polyxenie E, Grant, Maria B

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Inactivation of the Basigin gene impairs normal retinal development and maturation von Ochrietor, Judith D, Moroz, Tatiana P, Clamp, Michael F, Timmers, Adrian M, Muramatsu, Takashi, Linser, Paul J

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Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice von Song, Chunjuan, Conlon, Thomas J, Deng, Wen-Tao, Coleman, Kirsten E, Zhu, Ping, Plummer, Cayrn, Mandapati, Savitri, Van Hoosear, Mailin, Green, Kari B, Sonnentag, Peter, Sharma, Alok K, Timmers, Adrian, Robinson, Paulette M, Knop, David R, Hauswirth, William W, Chulay, Jeffrey D, Shearman, Mark S, Ye, Guo-Jie

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Noninvasive Imaging by Optical Coherence Tomography to Monitor Retinal Degeneration in the Mouse von Li, Qiuhong, Timmers, Adrian M, Hunter, Kirk, Gonzalez-Pola, Carlos, Lewin, Alfred S, Reitze, David H, Hauswirth, William W

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