Gene therapy using haematopoietic stem and progenitor cells von Ferrari, Giuliana, Thrasher, Adrian J., Aiuti, Alessandro

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Gene therapy: progress and predictions von Collins, Mary, Thrasher, Adrian

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Gene therapy for PIDs: Progress, pitfalls and prospects von Mukherjee, Sayandip, Thrasher, Adrian J.

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Wiskott‐Aldrich syndrome protein: Emerging mechanisms in immunity von Rivers, Elizabeth, Thrasher, Adrian J.

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Gene Editing for the Treatment of Primary Immunodeficiency Diseases von Rai, Rajeev, Thrasher, Adrian J., Cavazza, Alessia

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Gene therapy for primary immunodeficiency von Booth, Claire, Romano, Rosa, Roncarolo, Maria Grazia, Thrasher, Adrian J

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The cytoplasm of living cells behaves as a poroelastic material von Moeendarbary, Emad, Valon, Léo, Fritzsche, Marco, Harris, Andrew R., Moulding, Dale A., Thrasher, Adrian J., Stride, Eleanor, Mahadevan, L., Charras, Guillaume T.

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WASP: a key immunological multitasker von Thrasher, Adrian J, Burns, Siobhan O

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Cellular Control of Cortical Actin Nucleation von Bovellan, Miia, Romeo, Yves, Biro, Maté, Boden, Annett, Chugh, Priyamvada, Yonis, Amina, Vaghela, Malti, Fritzsche, Marco, Moulding, Dale, Thorogate, Richard, Jégou, Antoine, Thrasher, Adrian J., Romet-Lemonne, Guillaume, Roux, Philippe P., Paluch, Ewa K., Charras, Guillaume

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Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome von Rai, Rajeev, Romito, Marianna, Rivers, Elizabeth, Turchiano, Giandomenico, Blattner, Georges, Vetharoy, Winston, Ladon, Dariusz, Andrieux, Geoffroy, Zhang, Fang, Zinicola, Marta, Leon-Rico, Diego, Santilli, Giorgia, Thrasher, Adrian J., Cavazza, Alessia

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A robust model for read count data in exome sequencing experiments and implications for copy number variant calling von PLAGNOL, Vincent, CURTIS, James, KUMARARATNE, Dinakantha, DOFFINGER, Rainer, NEJENTSEV, Sergey, EPSTEIN, Michael, MOK, Kin Y, STEBBINGS, Emma, GRIGORIADOU, Sofia, WOOD, Nicholas W, HAMBLETON, Sophie, BURNS, Siobhan O, THRASHER, Adrian J

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Treating Immunodeficiency through HSC Gene Therapy von Booth, Claire, Gaspar, H. Bobby, Thrasher, Adrian J

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How I manage patients with Wiskott Aldrich syndrome von Rivers, Elizabeth, Worth, Austen, Thrasher, Adrian J., Burns, Siobhan O.

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Update on the hyper immunoglobulin M syndromes von Davies, E. Graham, Thrasher, Adrian J.

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Actin cytoskeletal defects in immunodeficiency von Moulding, Dale A., Record, Julien, Malinova, Dessislava, Thrasher, Adrian J.

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Allosteric inhibition of SHP2 rescues functional T-cell abnormalities in SAP deficiency von Panchal, Neelam, Houghton, Benjamin Christopher, Vassalou, Elina, Thrasher, Adrian J., Booth, Claire

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Gene therapy for X-linked severe combined immunodeficiency: Historical outcomes and current status von Pai, Sung-Yun, Thrasher, Adrian J.

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Biallelic JAK1 mutations in immunodeficient patient with mycobacterial infection von Eletto, Davide, Burns, Siobhan O., Angulo, Ivan, Plagnol, Vincent, Gilmour, Kimberly C., Henriquez, Frances, Curtis, James, Gaspar, Miguel, Nowak, Karolin, Daza-Cajigal, Vanessa, Kumararatne, Dinakantha, Doffinger, Rainer, Thrasher, Adrian J., Nejentsev, Sergey

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Differential Transgene Silencing of Myeloid-Specific Promoters in the AAVS1 Safe Harbor Locus of Induced Pluripotent Stem Cell-Derived Myeloid Cells von Klatt, Denise, Cheng, Erica, Hoffmann, Dirk, Santilli, Giorgia, Thrasher, Adrian J., Brendel, Christian, Schambach, Axel

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Lancet Commission: Stem cells and regenerative medicine von Cossu, Giulio, Birchall, Martin, Brown, Tracey, De Coppi, Paolo, Culme-Seymour, Emily, Gibbon, Sahra, Hitchcock, Julian, Mason, Chris, Montgomery, Jonathan, Morris, Steve, Muntoni, Francesco, Napier, David, Owji, Nazanin, Prasad, Aarathi, Round, Jeff, Saprai, Prince, Stilgoe, Jack, Thrasher, Adrian, Wilson, James

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